| Treatment of a mouse model of ALS by in vivo base editing CKW Lim, M Gapinske, AK Brooks, WS Woods, JE Powell, MA Zeballos C., ... Molecular Therapy 28 (4), 1177-1189, 2020 | 195 | 2020 |
| Targeted gene silencing in the nervous system with CRISPR-Cas13 JE Powell, CKW Lim, R Krishnan, TX McCallister, C Saporito-Magriña, ... Science Advances 8 (3), eabk2485, 2022 | 76 | 2022 |
| Next-Generation CRISPR Technologies and Their Applications in Gene and Cell Therapy MA Zeballos C, T Gaj Trends in Biotechnology 39 (7), 692-705, 2020 | 76* | 2020 |
| Nerve Growth Factor modulates LPS-induced microglial glycolysis and inflammatory responses G Fodelianaki, F Lansing, P Bhattarai, M Troullinaki, MA Zeballos, ... Experimental cell research 377 (1-2), 10-16, 2019 | 62 | 2019 |
| Valve leaflet‐inspired elastomeric scaffolds with tunable and anisotropic mechanical properties Y Xue, P Ravishankar, MA Zeballos, V Sant, K Balachandran, S Sant Polymers for Advanced Technologies 31 (1), 94-106, 2020 | 23 | 2020 |
| Isolation of endothelial progenitor cells from human umbilical cord blood P Ravishankar, MA Zeballos, K Balachandran JoVE (Journal of Visualized Experiments), e56021, 2017 | 23 | 2017 |
| Mitigating a TDP-43 proteinopathy by targeting ataxin-2 using RNA-targeting CRISPR effector proteins MA Zeballos C, HJ Moore, TJ Smith, JE Powell, NS Ahsan, S Zhang, T Gaj Nature Communications 14 (1), 6492, 2023 | 16 | 2023 |
| CRISPR base editing of cis-regulatory elements enables the perturbation of neurodegeneration-linked genes CKW Lim, TX McCallister, C Saporito-Magriña, GD McPheron, R Krishnan, ... Molecular Therapy 30 (12), 3619-3631, 2022 | 15 | 2022 |
| Treatment of a Mouse Model of ALS by CRISPR Base Editing CKW Lim, M Gapinske, AK Brooks, WS Woods, JE Powell, AC Zeballos, ... MOLECULAR THERAPY 28 (4), 406-406, 2020 | 2 | 2020 |
| SPLICER: A Highly Efficient Base Editing Toolbox That Enables In Vivo Therapeutic Exon Skipping A Miskalis, S Shirguppe, J Winter, G Elias, D Swami, A Nambiar, M Stilger, ... bioRxiv, 2024.04. 01.587650, 2024 | 1 | 2024 |
| CRISPR-Cas13-Mediated Knockdown of Ataxin-2 in a Stress Granule Cell Model and a TDP-43 Rodent Model MAC Zeballos, H Moore, JE Powell, T Gaj MOLECULAR THERAPY 29 (4), 281-281, 2021 | 1 | 2021 |
| CRISPR base editing of cis-regulatory elements enables target gene perturbations CKW Lim, TX McCallister, C Saporito-Magriña, GD McPheron, R Krishnan, ... bioRxiv, 2022.05. 26.493649, 2022 | | 2022 |
| Development of Platforms to Target HTT In Vivo Using Base Editing Technologies S Shirguppe, M Gapinske, D Swami, P Acharya, D Anand, D Joulani, ... MOLECULAR THERAPY 30 (4), 298-298, 2022 | | 2022 |
| Lowering Huntingtin Gene Expression by Targeted Base Editing of Cis-Regulatory Elements in its Promoter Sequence TX McCallister, CKW Lim, C Saporito-Magrina, R Krishnan, GD McPheron, ... MOLECULAR THERAPY 30 (4), 390-390, 2022 | | 2022 |
| Targeted Gene Knockdown in the Brain and Spinal Cord by CRISPR-Cas13 CKW Lim, JE Powell, R Krishnan, TX McCallister, C Saporito-Magrina, ... MOLECULAR THERAPY 30 (4), 300-300, 2022 | | 2022 |
| Modulating Stress Granule Formation for Treatment of ALS via CRISPR-Cas13-Mediated Knockdown of Ataxin-2 MAC Zeballos, JE Powell, T Gaj MOLECULAR THERAPY 28 (4), 483-483, 2020 | | 2020 |
| AAV-Mediated Delivery of Single Base Editors Using Intein Trans-Splicing JS Winter, A Luu, A Zeballos, M Gapinske, WS Woods, T Gaj, JS Song, ... MOLECULAR THERAPY 27 (4), 106-107, 2019 | | 2019 |
| Effects of Uniaxial Cyclic Strain on Endothelial Progenitor Cells MA Zeballos Castro | | 2017 |