| Safety and efficacy of gene transfer for Leber's congenital amaurosis AM Maguire, F Simonelli, EA Pierce, EN Pugh Jr, F Mingozzi, J Bennicelli, ... New England Journal of Medicine 358 (21), 2240-2248, 2008 | 2650 | 2008 |
| Efficacy and safety of voretigene neparvovec (AAV2-hRPE65v2) in patients with RPE65-mediated inherited retinal dystrophy: a randomised, controlled, open-label, phase 3 trial S Russell, J Bennett, JA Wellman, DC Chung, ZF Yu, A Tillman, J Wittes, ... The Lancet 390 (10097), 849-860, 2017 | 1849 | 2017 |
| Gene therapy restores vision in a canine model of childhood blindness GM Acland, GD Aguirre, J Ray, Q Zhang, TS Aleman, AV Cideciyan, ... Nature genetics 28 (1), 92-95, 2001 | 1558 | 2001 |
| Age-dependent effects of RPE65 gene therapy for Leber's congenital amaurosis: a phase 1 dose-escalation trial AM Maguire, KA High, A Auricchio, JF Wright, EA Pierce, F Testa, ... The Lancet 374 (9701), 1597-1605, 2009 | 1082 | 2009 |
| Small interfering RNA (siRNA) targeting VEGF effectively inhibits ocular neovascularization in a mouse model SJ Reich, J Fosnot, A Kuroki, W Tang, X Yang, AM Maguire, J Bennett, ... Mol Vis 9 (5), 210-216, 2003 | 773 | 2003 |
| Gene therapy for Leber's congenital amaurosis is safe and effective through 1.5 years after vector administration F Simonelli, AM Maguire, F Testa, EA Pierce, F Mingozzi, JL Bennicelli, ... Molecular Therapy 18 (3), 643-650, 2010 | 734 | 2010 |
| Lateral connectivity and contextual interactions in macaque primary visual cortex DD Stettler, A Das, J Bennett, CD Gilbert Neuron 36 (4), 739-750, 2002 | 601 | 2002 |
| Long-term restoration of rod and cone vision by single dose rAAV-mediated gene transfer to the retina in a canine model of childhood blindness GM Acland, GD Aguirre, J Bennett, TS Aleman, AV Cideciyan, J Bennicelli, ... Molecular Therapy 12 (6), 1072-1082, 2005 | 583 | 2005 |
| Mutation of a nuclear receptor gene, NR2E3, causes enhanced S cone syndrome, a disorder of retinal cell fate NB Haider, SG Jacobson, AV Cideciyan, R Swiderski, LM Streb, C Searby, ... Nature genetics 24 (2), 127-131, 2000 | 530 | 2000 |
| Safety and durability of effect of contralateral-eye administration of AAV2 gene therapy in patients with childhood-onset blindness caused by RPE65 mutations: a follow-on phase … J Bennett, J Wellman, KA Marshall, S McCague, M Ashtari, ... The Lancet 388 (10045), 661-672, 2016 | 523 | 2016 |
| A locus control region adjacent to the human red and green visual pigment genes Y Wang, JP Macke, SL Merbs, DJ Zack, B Klaunberg, J Bennett, ... Neuron 9 (3), 429-440, 1992 | 487 | 1992 |
| AAV2 gene therapy readministration in three adults with congenital blindness J Bennett, M Ashtari, J Wellman, KA Marshall, LL Cyckowski, DC Chung, ... Science translational medicine 4 (120), 120ra15-120ra15, 2012 | 484 | 2012 |
| Exchange of surface proteins impacts on viral vector cellular specificity and transduction characteristics: the retina as a model A Auricchio, G Kobinger, V Anand, M Hildinger, E O'Connor, AM Maguire, ... Human molecular genetics 10 (26), 3075-3081, 2001 | 474 | 2001 |
| Photoreceptor cell rescue in retinal degeneration (rd) mice by in vivo gene therapy J Bennett, T Tanabe, D Sun, Y Zeng, H Kjeldbye, P Gouras, AM Maguire Nature medicine 2 (6), 649-654, 1996 | 417 | 1996 |
| Three-year follow-up after unilateral subretinal delivery of adeno-associated virus in patients with Leber congenital Amaurosis type 2 F Testa, AM Maguire, S Rossi, EA Pierce, P Melillo, K Marshall, S Banfi, ... Ophthalmology 120 (6), 1283-1291, 2013 | 414 | 2013 |
| Serotype-dependent packaging of large genes in adeno-associated viral vectors results in effective gene delivery in mice M Allocca, M Doria, M Petrillo, P Colella, M Garcia-Hoyos, D Gibbs, ... The Journal of clinical investigation 118 (5), 1955-1964, 2008 | 364 | 2008 |
| Efficacy, safety, and durability of voretigene neparvovec-rzyl in RPE65 mutation–associated inherited retinal dystrophy: results of phase 1 and 3 trials AM Maguire, S Russell, JA Wellman, DC Chung, ZF Yu, A Tillman, ... Ophthalmology 126 (9), 1273-1285, 2019 | 353 | 2019 |
| Adenovirus vector-mediated in vivo gene transfer into adult murine retina. J Bennett, J Wilson, D Sun, B Forbes, A Maguire Investigative ophthalmology & visual science 35 (5), 2535-2542, 1994 | 335 | 1994 |
| Reversal of blindness in animal models of leber congenital amaurosis using optimized AAV2-mediated gene transfer J Bennicelli, JF Wright, A Komaromy, JB Jacobs, B Hauck, O Zelenaia, ... Molecular Therapy 16 (3), 458-465, 2008 | 328 | 2008 |
| Stable transgene expression in rod photoreceptors after recombinant adeno-associated virus-mediated gene transfer to monkey retina J Bennett, AM Maguire, AV Cideciyan, M Schnell, E Glover, V Anand, ... Proceedings of the National Academy of Sciences 96 (17), 9920-9925, 1999 | 307 | 1999 |
