WFH guidelines for the management of hemophilia A Srivastava, E Santagostino, A Dougall, S Kitchen, M Sutherland, ... Haemophilia 26, 1-158, 2020 | 1704 | 2020 |
Antioxidants reduce endoplasmic reticulum stress and improve protein secretion JD Malhotra, H Miao, K Zhang, A Wolfson, S Pennathur, SW Pipe, ... Proceedings of the National Academy of Sciences 105 (47), 18525-18530, 2008 | 798 | 2008 |
Efficacy, safety, and pharmacokinetics of emicizumab prophylaxis given every 4 weeks in people with haemophilia A (HAVEN 4): a multicentre, open-label, non-randomised phase 3 study SW Pipe, M Shima, M Lehle, A Shapiro, S Chebon, K Fukutake, NS Key, ... The Lancet Haematology 6 (6), e295-e305, 2019 | 398 | 2019 |
Bleeding due to disruption of a cargo-specific ER-to-Golgi transport complex B Zhang, MA Cunningham, WC Nichols, JA Bernat, U Seligsohn, SW Pipe, ... Nature genetics 34 (2), 220-225, 2003 | 333 | 2003 |
International workshop on immune tolerance induction: consensus recommendations1 DM DIMICHELE, WK Hoots, SW Pipe, GE Rivard, E Santagostino Haemophilia 13, 1-22, 2007 | 324 | 2007 |
Valoctocogene roxaparvovec gene therapy for hemophilia A MC Ozelo, J Mahlangu, KJ Pasi, A Giermasz, AD Leavitt, M Laffan, ... New England Journal of Medicine 386 (11), 1013-1025, 2022 | 323 | 2022 |
Bioengineering of coagulation factor VIII for improved secretion HZ Miao, N Sirachainan, L Palmer, P Kucab, MA Cunningham, ... Blood 103 (9), 3412-3419, 2004 | 299 | 2004 |
Long-term outcomes with emicizumab prophylaxis for hemophilia A with or without FVIII inhibitors from the HAVEN 1-4 studies MU Callaghan, C Negrier, I Paz-Priel, T Chang, S Chebon, M Lehle, ... Blood, The Journal of the American Society of Hematology 137 (16), 2231-2242, 2021 | 252 | 2021 |
Life in the shadow of a dominant partner: the FVIII-VWF association and its clinical implications for hemophilia A SW Pipe, RR Montgomery, KP Pratt, PJ Lenting, D Lillicrap Blood, The Journal of the American Society of Hematology 128 (16), 2007-2016, 2016 | 235 | 2016 |
Differential interaction of coagulation factor VIII and factor V with protein chaperones calnexin and calreticulin SW Pipe, JA Morris, J Shah, RJ Kaufman Journal of Biological Chemistry 273 (14), 8537-8544, 1998 | 214 | 1998 |
Gene therapy with etranacogene dezaparvovec for hemophilia B SW Pipe, FWG Leebeek, M Recht, NS Key, G Castaman, W Miesbach, ... New England Journal of Medicine 388 (8), 706-718, 2023 | 212 | 2023 |
New therapies for hemophilia AC Weyand, SW Pipe Blood, The Journal of the American Society of Hematology 133 (5), 389-398, 2019 | 192 | 2019 |
Mannose-dependent endoplasmic reticulum (ER)-Golgi intermediate compartment-53-mediated ER to Golgi trafficking of coagulation factors V and VIII M Moussalli, SW Pipe, HP Hauri, WC Nichols, D Ginsburg, RJ Kaufman Journal of Biological Chemistry 274 (46), 32539-32542, 1999 | 168 | 1999 |
Functional roles of the factor VIII B domain SW Pipe Haemophilia 15 (6), 1187-1196, 2009 | 157 | 2009 |
Mutagenesis of a potential immunoglobulin-binding protein-binding site enhances secretion of coagulation factor VIII M Swaroop, M Moussalli, SW Pipe, RJ Kaufman Journal of Biological Chemistry 272 (39), 24121-24124, 1997 | 152 | 1997 |
Characterization of a genetically engineered inactivation-resistant coagulation factor VIIIa SW Pipe, RJ Kaufman Proceedings of the National Academy of Sciences 94 (22), 11851-11856, 1997 | 151 | 1997 |
Recombinant clotting factors SW Pipe Thrombosis and haemostasis 99 (11), 840-850, 2008 | 150 | 2008 |
Two-year outcomes of valoctocogene roxaparvovec therapy for hemophilia A J Mahlangu, R Kaczmarek, A Von Drygalski, S Shapiro, SC Chou, ... New England Journal of Medicine 388 (8), 694-705, 2023 | 147 | 2023 |
Four hydrophobic amino acids of the factor VIII C2 domain are constituents of both the membrane-binding and von Willebrand factor-binding motifs GE Gilbert, RJ Kaufman, AA Arena, H Miao, SW Pipe Journal of Biological Chemistry 277 (8), 6374-6381, 2002 | 147 | 2002 |
Effects and interferences of emicizumab, a humanised bispecific antibody mimicking activated factor VIII cofactor function, on coagulation assays JI Adamkewicz, DC Chen, I Paz-Priel Thrombosis and haemostasis 119 (07), 1084-1093, 2019 | 139 | 2019 |