| Preparation for a first-in-man lentivirus trial in patients with cystic fibrosis EWFW Alton, JM Beekman, AC Boyd, J Brand, MS Carlon, MM Connolly, ... Thorax 72 (2), 137-147, 2017 | 178 | 2017 |
| Efficient and stable transduction of dopaminergic neurons in rat substantia nigra by rAAV 2/1, 2/2, 2/5, 2/6.2, 2/7, 2/8 and 2/9 A Van der Perren, J Toelen, M Carlon, C Van den Haute, F Coun, ... Gene therapy 18 (5), 517-527, 2011 | 116 | 2011 |
| Fetal surgery is a clinical reality JA Deprest, R Devlieger, K Srisupundit, V Beck, I Sandaite, S Rusconi, ... Seminars in fetal and neonatal medicine 15 (1), 58-67, 2010 | 102 | 2010 |
| Allele specific repair of splicing mutations in cystic fibrosis through AsCas12a genome editing G Maule, A Casini, C Montagna, AS Ramalho, K De Boeck, Z Debyser, ... Nature communications 10 (1), 3556, 2019 | 99 | 2019 |
| FK506 reduces neuroinflammation and dopaminergic neurodegeneration in an α-synuclein-based rat model for Parkinson's disease A Van der Perren, F Macchi, J Toelen, MS Carlon, M Maris, H de Loor, ... Neurobiology of aging 36 (3), 1559-1568, 2015 | 88 | 2015 |
| rAAV-CFTRΔR rescues the cystic fibrosis phenotype in human intestinal organoids and cystic fibrosis mice D Vidović, MS Carlon, MF Da Cunha, JF Dekkers, MI Hollenhorst, ... American Journal of Respiratory and Critical Care Medicine 193 (3), 288-298, 2016 | 72 | 2016 |
| Amniotic fluid derived stem cells with a renal progenitor phenotype inhibit interstitial fibrosis in renal ischemia and reperfusion injury in rats MG Monteiro Carvalho Mori da Cunha, S Zia, F Oliveira Arcolino, ... PloS one 10 (8), e0136145, 2015 | 50 | 2015 |
| Protection of pigs against Chlamydia trachomatis challenge by administration of a MOMP-based DNA vaccine in the vaginal mucosa K Schautteet, E Stuyven, DSA Beeckman, S Van Acker, M Carlon, ... Vaccine 29 (7), 1399-1407, 2011 | 43 | 2011 |
| Efficient gene transfer into the mouse lung by fetal intratracheal injection of rAAV2/6.2 M Carlon, J Toelen, A Van der Perren, LH Vandenberghe, V Reumers, ... Molecular Therapy 18 (12), 2130-2138, 2010 | 40 | 2010 |
| Assays of CFTR function in vitro, ex vivo and in vivo AS Ramalho, M Boon, M Proesmans, F Vermeulen, MS Carlon, ... International journal of molecular sciences 23 (3), 1437, 2022 | 37 | 2022 |
| Phenotyping of Rare CFTR Mutations Reveals Distinct Trafficking and Functional Defects M Ensinck, L De Keersmaecker, L Heylen, AS Ramalho, R Gijsbers, ... Cells 9 (3), 754, 2020 | 33 | 2020 |
| Novel CFTR modulator combinations maximise rescue of G85E and N1303K in rectal organoids MM Ensinck, L De Keersmaecker, AS Ramalho, S Cuyx, S Van Biervliet, ... ERJ Open Research 8 (2), 2022 | 29 | 2022 |
| One size does not fit all: the past, present and future of cystic fibrosis causal therapies MM Ensinck, MS Carlon Cells 11 (12), 1868, 2022 | 26 | 2022 |
| Vascular endothelial growth factor up-regulation in human amniotic fluid stem cell enhances nephroprotection after ischemia-reperfusion injury in the rat S Zia, DV Beckmann, MS Carlon, FO Arcolino, M Albersen, NL Pippi, ... Critical care medicine 45 (1), e86-e96, 2017 | 26 | 2017 |
| On the corner of models and cure: gene editing in cystic fibrosis M Ensinck, A Mottais, C Detry, T Leal, MS Carlon Frontiers in pharmacology 12, 662110, 2021 | 24 | 2021 |
| Roadmap for an early gene therapy for cystic fibrosis airway disease MS Carlon, D Vidović, S Birket Prenatal Diagnosis 37 (12), 1181-1190, 2017 | 22 | 2017 |
| Immunological ignorance allows long-term gene expression after perinatal recombinant adeno-associated virus-mediated gene transfer to murine airways MS Carlon, D Vidović, J Dooley, MM da Cunha, M Maris, Y Lampi, ... Human Gene Therapy 25 (6), 517-528, 2014 | 22 | 2014 |
| Transcriptomic analysis of CFTR-impaired endothelial cells reveals a pro-inflammatory phenotype M Declercq, P de Zeeuw, NV Conchinha, V Geldhof, AS Ramalho, ... European Respiratory Journal 57 (4), 2021 | 21 | 2021 |
| Functional restoration of a CFTR splicing mutation through RNA delivery of CRISPR adenine base editor S Amistadi, G Maule, M Ciciani, MM Ensinck, L De Keersmaecker, ... Molecular Therapy 31 (6), 1647-1660, 2023 | 17 | 2023 |
| Noninvasive imaging reveals stable transgene expression in mouse airways after delivery of a nonintegrating recombinant adeno-associated viral vector D Vidović, R Gijsbers, A Quiles-Jimenez, J Dooley, C Van den Haute, ... Human gene therapy 27 (1), 60-71, 2016 | 17 | 2016 |
