| An evolved AAV variant enables efficient genetic engineering of murine T cells WA Nyberg, J Ark, A To, S Clouden, G Reeder, JJ Muldoon, JY Chung, ... Cell 186 (2), 446-460. e19, 2023 | 50 | 2023 |
| Rescue of glutaric aciduria type I in mice by liver-directed therapies M Barzi, CG Johnson, T Chen, RM Rodriguiz, M Hemmingsen, ... Science translational medicine 15 (692), eadf4086, 2023 | 11 | 2023 |
| Repurposing CRISPR-Cas13 systems for robust mRNA trans-splicing DN Fiflis, NA Rey, H Venugopal-Lavanya, B Sewell, A Mitchell-Dick, ... Nature Communications 15 (1), 2325, 2024 | 8 | 2024 |
| The HIV protease inhibitor darunavir prevents kidney injury via HIV-independent mechanisms X Gao, A Rosales, H Karttunen, GM Bommana, B Tandoh, Z Yi, Z Habib, ... Scientific reports 9 (1), 15857, 2019 | 7 | 2019 |
| Capsid-mediated control of adeno-associated viral transcription determines host range EJ Loeb, PL Havlik, ZC Elmore, A Rosales, SM Fergione, TJ Gonzalez, ... Cell reports 43 (3), 2024 | 5 | 2024 |
| Engineered IgM and IgG cleaving enzymes for mitigating antibody neutralization and complement activation in AAV gene transfer TJ Smith, ZC Elmore, RM Fusco, JA Hull, A Rosales, M Martinez, ... Molecular Therapy, 2024 | 4 | 2024 |
| A humanized mouse model for adeno-associated viral gene therapy M Barzi, T Chen, TJ Gonzalez, FP Pankowicz, SH Oh, HL Streff, ... Nature Communications 15 (1), 1955, 2024 | 4 | 2024 |
| Evolving adeno-associated viruses for gene transfer to the kidney via cross-species cycling of capsid libraries A Rosales, LO Blondel, J Hull, Q Gao, N Aykun, JL Peek, A Vargas, ... Nature Biomedical Engineering, 1-15, 2025 | | 2025 |
| In vivo engineering of murine T cells using the evolved adeno-associated virus variant Ark313 WA Nyberg, CH Wang, J Ark, C Liu, S Clouden, A Qualls, S Caryotakis, ... Immunity, 2025 | | 2025 |
| Proximal Tubule-Targeted Adeno-Associated Virus (AAV) Gene Therapy for Cystinuria: SA-PO647 JL Peek, A Rosales, J Qi, A Menshikh, RC Welch, F Bock, LE Woodard, ... Journal of the American Society of Nephrology 35 (10S), 10.1681, 2024 | | 2024 |
| Sub-genomic flaviviral RNA elements increase the stability and abundance of recombinant AAV vector transcripts RM Meganck, R Ogurlu, J Liu, S Moller-Tank, V Tse, LO Blondel, ... Journal of Virology 98 (8), e00095-24, 2024 | | 2024 |
| 739 TREATMENT OF CYSTIC FIBROSIS WITH IN VIVO BASE EDITING OF THE INTESTINAL EPITHELIUM B Sheahan, O Kislovskiy, V Thiriveedi, S Khumukcham, A Rosales, ... Gastroenterology 164 (6), S-151, 2023 | | 2023 |
| Enhanced CRISPR/Cas9 Genome Editing in Heart and Skeletal Muscle with a Potent New AAV Variant TJ Gonzalez, L Blondel, A Rosales, H Daniels, CA Gersbach, A Asokan MOLECULAR THERAPY 30 (4), 211-212, 2022 | | 2022 |
| Targeted In Vivo Manipulation of Murine T-Cells Using a Newly Evolved AAV Capsid Mutant JI Ark, W Nyberg, K Simon, A Rosales, S Clouden, J Eyquem, A Asokan MOLECULAR THERAPY 30 (4), 425-426, 2022 | | 2022 |
| Novel Gene Supplementation, Genome Editing and Cellular Therapeutic Approaches to Treat Glutaric Aciduria Type I M Barzi, C Johnson, T Chen, M Hemmingsen, A El-Gharbawy, ... MOLECULAR THERAPY 30 (4), 458-458, 2022 | | 2022 |
| A Newly Evolved AAV Variant Enables Potent Gene Transfer in Kidneys of Multiple Species A Rosales, T Gonzalez, A Asokan MOLECULAR THERAPY 30 (4), 555-555, 2022 | | 2022 |
| The HIV protease inhibitor darunavir prevents kidney injury via HIV-independent mechanisms (vol 9, 15857, 2019) X Gao, A Rosales, H Karttunen, GM Bommana, B Tandoh, Z Yi, Z Habib, ... SCIENTIFIC REPORTS 10 (1), 2020 | | 2020 |
| Publisher Correction: The HIV protease inhibitor darunavir prevents kidney injury via HIV-independent mechanisms X Gao, A Rosales, H Karttunen, GM Bommana, B Tandoh, Z Yi, Z Habib, ... Scientific reports 10, 2020 | | 2020 |
