| Organoids and microphysiological systems: Promising models for accelerating AAV gene therapy studies RM Ramamurthy, A Atala, CD Porada, G Almeida-Porada Frontiers in immunology 13, 1011143, 2022 | 18 | 2022 |
| Defining the optimal FVIII transgene for placental cell-based gene therapy to treat hemophilia A N El-Akabawy, M Rodriguez, R Ramamurthy, A Rabah, B Trevisan, ... Molecular Therapy Methods & Clinical Development 17, 465-477, 2020 | 14 | 2020 |
| Investigating optimal autologous cellular platforms for prenatal or perinatal factor VIII delivery to treat hemophilia a C Stem, C Rodman, RM Ramamurthy, S George, D Meares, A Farland, ... Frontiers in Cell and Developmental Biology 9, 678117, 2021 | 6 | 2021 |
| Administration of Cells Engineered to Secrete Fviii-mcoET3 in Prenatal Sheep Recipients Results in Sustained Curative Fviii Plasma Levels for 3 Years after Birth, without … M Rodriguez, B Trevisan, S George, RM Ramamurthy, A Rabah, ... Blood 136, 1-2, 2020 | 3 | 2020 |
| Comparison of different gene addition strategies to modify placental derived-mesenchymal stromal cells to produce FVIII RM Ramamurthy, M Rodriguez, HC Ainsworth, J Shields, D Meares, ... Frontiers in Immunology 13, 954984, 2022 | 2 | 2022 |
| Using a human liver tissue equivalent (hLTE) platform to define the functional impact of liver-directed AAV gene therapy RM Ramamurthy, WT Zheng, S George, M Wan, Y Zhou, B Lu, CE Bishop, ... Blood 138 (Supplement 1), 2938-2938, 2021 | 2 | 2021 |
| Targeted CRISPR/Cas9-mediated gene addition to a safe harbor in placental cells for the treatment of hemophilia A RM Ramamurthy, M Rodriguez, D Meares, A Farland, A Atala, ... MOLECULAR THERAPY 28 (4), 351-351, 2020 | 1 | 2020 |
| Transplanting FVIII/ET3-secreting cells in fetal sheep increases FVIII levels long-term without inducing immunity or toxicity M Rodriguez, B Trevisan, RM Ramamurthy, SK George, J Diaz, ... Nature Communications 14 (1), 4206, 2023 | | 2023 |
| Human Liver Tissue Equivalents (hLTEs): A Novel Platform for Studying the Impact of AAV Gene Therapy on the Liver RM Ramamurthy, WT Zheng, SK George, M Wan, Y Zhou, B Lu, ... MOLECULAR THERAPY 30 (4), 246-247, 2022 | | 2022 |
| Evaluation of Maternal Safety Following Prenatal Cell and Gene Therapy for Hemophilia a in a Large Animal Model Demonstrates Absence of Maternal Exposure to the Cells or Gene … QDM Pham, M Rodriguez, RM Ramamurthy, S George, J Figueroa, ... Blood 136, 32, 2020 | | 2020 |
| Synovial Gene Therapy for Hemarthrosis in Patients with Hemophilia A S George, H Medder, R Ramamurthy, B Trevisan, J Shields, D Meares, ... MOLECULAR THERAPY 28 (4), 362-362, 2020 | | 2020 |
| Integration Site Analysis in a Pre-Clinical Trial of Lentivector-Modified hPLC Gene Therapy for Hemophilia A Shows Polyclonality and No Signs of Genotoxicity A Rabah, M Rodriguez, R Ramamurthy, A Atala, HT Spencer, CB Doering, ... MOLECULAR THERAPY 27 (4), 154-155, 2019 | | 2019 |
