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Defibrotide for prophylaxis of hepatic veno-occlusive disease in paediatric haemopoietic stem-cell transplantation: an open-label, phase 3, randomised controlled trial S Corbacioglu, S Cesaro, M Faraci, D Valteau-Couanet, B Gruhn, ... The Lancet 379 (9823), 1301-1309, 2012 | 430 | 2012 |
Defective cytotoxic lymphocyte degranulation in syntaxin-11–deficient familial hemophagocytic lymphohistiocytosis 4 (FHL4) patients YT Bryceson, E Rudd, C Zheng, J Edner, D Ma, SM Wood, ... Blood, The Journal of the American Society of Hematology 110 (6), 1906-1915, 2007 | 378 | 2007 |
Neutrophils kill antibody-opsonized cancer cells by trogoptosis HL Matlung, L Babes, XW Zhao, M van Houdt, LW Treffers, DJ van Rees, ... Cell reports 23 (13), 3946-3959. e6, 2018 | 374 | 2018 |
Long-term outcome of Hurler syndrome patients after hematopoietic cell transplantation: an international multicenter study M Aldenhoven, RF Wynn, PJ Orchard, A O’Meara, P Veys, A Fischer, ... Blood, The Journal of the American Society of Hematology 125 (13), 2164-2172, 2015 | 357 | 2015 |
Association between anti-thymocyte globulin exposure and CD4+ immune reconstitution in paediatric haemopoietic cell transplantation: a multicentre, retrospective … R Admiraal, C van Kesteren, CM Jol-van der Zijde, AC Lankester, ... The Lancet Haematology 2 (5), e194-e203, 2015 | 283 | 2015 |
Outcomes of hematopoietic stem cell transplantation for Hurler's syndrome in Europe: a risk factor analysis for graft failure JJ Boelens, RF Wynn, A O'meara, P Veys, Y Bertrand, G Souillet, ... Bone marrow transplantation 40 (3), 225-233, 2007 | 281 | 2007 |
Enzyme replacement therapy and/or hematopoietic stem cell transplantation at diagnosis in patients with mucopolysaccharidosis type I: results of a European consensus procedure MH de Ru, JJ Boelens, AM Das, SA Jones, JH van der Lee, N Mahlaoui, ... Orphanet journal of rare diseases 6, 1-9, 2011 | 277 | 2011 |
Toxicity and response after CD19-specific CAR T-cell therapy in pediatric/young adult relapsed/refractory B-ALL KJ Curran, SP Margossian, NA Kernan, LB Silverman, DA Williams, ... Blood, The Journal of the American Society of Hematology 134 (26), 2361-2368, 2019 | 264 | 2019 |
How I treat adenovirus in hematopoietic stem cell transplant recipients CA Lindemans, AM Leen, JJ Boelens Blood, The Journal of the American Society of Hematology 116 (25), 5476-5485, 2010 | 264 | 2010 |
Association of busulfan exposure with survival and toxicity after haemopoietic cell transplantation in children and young adults: a multicentre, retrospective cohort analysis IH Bartelink, A Lalmohamed, EML van Reij, CC Dvorak, RM Savic, ... The Lancet Haematology 3 (11), e526-e536, 2016 | 263 | 2016 |
The clinical outcome of Hurler syndrome after stem cell transplantation M Aldenhoven, JJ Boelens, TJ de Koning Biology of Blood and Marrow Transplantation 14 (5), 485-498, 2008 | 237 | 2008 |
Association between anti-thymocyte globulin exposure and survival outcomes in adult unrelated haemopoietic cell transplantation: a retrospective, pharmacodynamic cohort analysis R Admiraal, S Nierkens, MA de Witte, EJ Petersen, G Fleurke, L Verrest, ... The Lancet Haematology 4 (4), e183-e191, 2017 | 222 | 2017 |
Outcomes of transplantation using various hematopoietic cell sources in children with Hurler syndrome after myeloablative conditioning JJ Boelens, M Aldenhoven, D Purtill, A Ruggeri, T DeFor, R Wynn, ... Blood, The Journal of the American Society of Hematology 121 (19), 3981-3987, 2013 | 217 | 2013 |
Anakinra for flares of pyogenic arthritis in PAPA syndrome MP Dierselhuis, J Frenkel, NM Wulffraat, JJ Boelens Rheumatology 44 (3), 406-a-406-a, 2005 | 217 | 2005 |
Metachromatic leukodystrophy: Disease spectrum and approaches for treatment DF Van Rappard, JJ Boelens, NI Wolf Best Practice & Research Clinical Endocrinology & Metabolism 29 (2), 261-273, 2015 | 213 | 2015 |
Impact of thymoglobulin prior to pediatric unrelated umbilical cord blood transplantation on immune reconstitution and clinical outcome CA Lindemans, R Chiesa, PJ Amrolia, K Rao, O Nikolajeva, A de Wildt, ... Blood, The Journal of the American Society of Hematology 123 (1), 126-132, 2014 | 198 | 2014 |
Outcome of hematopoietic stem cell transplantation for adenosine deaminase–deficient severe combined immunodeficiency A Hassan, C Booth, A Brightwell, Z Allwood, P Veys, K Rao, M Hönig, ... Blood, The Journal of the American Society of Hematology 120 (17), 3615-3624, 2012 | 180 | 2012 |
Hematopoietic stem cell transplantation for mucopolysaccharidoses: past, present, and future M Taylor, S Khan, M Stapleton, J Wang, J Chen, R Wynn, H Yabe, ... Biology of Blood and Marrow Transplantation 25 (7), e226-e246, 2019 | 178 | 2019 |
Excellent T-cell reconstitution and survival depend on low ATG exposure after pediatric cord blood transplantation R Admiraal, CA Lindemans, C van Kesteren, MB Bierings, AB Versluijs, ... Blood, The Journal of the American Society of Hematology 128 (23), 2734-2741, 2016 | 174 | 2016 |