| Correction of the sickle cell disease mutation in human hematopoietic stem/progenitor cells MD Hoban, GJ Cost, MC Mendel, Z Romero, ML Kaufman, AV Joglekar, ... Blood, The Journal of the American Society of Hematology 125 (17), 2597-2604, 2015 | 391 | 2015 |
| CRISPR/Cas9-mediated correction of the sickle mutation in human CD34+ cells MD Hoban, D Lumaquin, CY Kuo, Z Romero, J Long, M Ho, CS Young, ... Molecular Therapy 24 (9), 1561-1569, 2016 | 231 | 2016 |
| High throughput sequencing analysis of RNA libraries reveals the influences of initial library and PCR methods on SELEX efficiency M Takahashi, X Wu, M Ho, P Chomchan, JJ Rossi, JC Burnett, J Zhou Scientific reports 6 (1), 1-14, 2016 | 114 | 2016 |
| Genetic regulation of OAS1 nonsense-mediated decay underlies association with COVID-19 hospitalization in patients of European and African ancestries AR Banday, ML Stanifer, O Florez-Vargas, OO Onabajo, BW Papenberg, ... Nature Genetics, 1-14, 2022 | 104 | 2022 |
| AptaTRACE Elucidates RNA Sequence-Structure Motifs from Selection Trends in HT-SELEX Experiments P Dao, J Hoinka, M Takahashi, J Zhou, M Ho, Y Wang, F Costa, JJ Rossi, ... Cell Systems 3 (1), 62-70, 2016 | 77 | 2016 |
| HSV-sr39TK positron emission tomography and suicide gene elimination of human hematopoietic stem cells and their progeny in humanized mice EH Gschweng, MN McCracken, ML Kaufman, M Ho, RP Hollis, X Wang, ... Cancer research 74 (18), 5173-5183, 2014 | 41 | 2014 |
| Dissecting the Mechanism of Histone Deacetylase Inhibitors to Enhance the Activity of Zinc Finger Nucleases Delivered by Integrase-Defective Lentiviral Vectors AV Joglekar, L Stein, M Ho, MD Hoban, RP Hollis, DB Kohn Human gene therapy 25 (7), 599-608, 2014 | 23 | 2014 |
| Anti-CD19 Chimeric Antigen Receptor Controlled By The Suicide Gene HSVsr39TK In Hematopoietic Stem Cells For Immunotherapy Of B-Lineage Malignancies SM Larson, A Tu, S Senadheera, M Ho, DB Kohn, S deOliveira Blood, The Journal of the American Society of Hematology 122 (21), 1659-1659, 2013 | 19 | 2013 |
| Genetic regulation of OAS1 nonsense-mediated decay underlies association with risk of severe COVID-19 AR Banday, ML Stanifer, O Florez-Vargas, OO Onabajo, MA Zahoor, ... Medrxiv, 2021 | 12 | 2021 |
| 338. Evaluation of TALENs and the CRISPR/Cas9 Nuclease System To Correct the Sickle Cell Disease Mutation MD Hoban, D Lumaquin, C Kuo, Z Romero, C Young, M Ho, J Long, ... Molecular Therapy 23, S135, 2015 | 3 | 2015 |
| Genetic regulation of TERT splicing affects cancer risk by altering cellular longevity and replicative potential O Florez-Vargas, M Ho, MH Hogshead, BW Papenberg, CH Lee, ... Nature Communications 16 (1), 1-20, 2025 | | 2025 |
| Epidemiology meets epitranscriptomics: Exploring the cancer-related role of a novel TERT-antisense transcript and its regulation by RNA methylation BW Papenberg, O Florez-Vargas, M Ho, K Forsythe, C Zhang, CH Lee, ... Cancer Research 84 (6_Supplement), 7082-7082, 2024 | | 2024 |
| Exploring the role of a TERT intronic tandem repeat in regulating cell proliferative responses to environmental factors and cancer risk M Ho, O Florez-Vargas, M Hogshead, B Papenberg, CH Lee, C Zhang, ... Cancer Research 84 (6_Supplement), 1644-1644, 2024 | | 2024 |
| A polymorphic TERT tandem repeat creating an expandable intronic G4 quadruplex is associated with TERT expression, relative leukocyte telomere length and … O Florez-Vargas, M Ho, M Hogshead, CH Lee, K Forsythe, B Papenberg, ... Cancer Research 84 (6_Supplement), 6144-6144, 2024 | | 2024 |
| Genetic regulation of TERT splicing contributes to reduced or elevated cancer risk by altering cellular longevity and replicative potential O Florez-Vargas, M Ho, M Hogshead, CH Lee, BW Papenberg, ... medRxiv, 2024.11. 04.24316722, 2024 | | 2024 |
| Development of a CRISPR/Cas9 System for Mitochondrial Diseases M Ho, AH Pham, JJ Rossi, JC Burnett MOLECULAR THERAPY 28 (4), 39-40, 2020 | | 2020 |
| Site-Specific Correction of the Sickle Mutation in CD34+ Cells Using Zinc Finger Nucleases MD Hoban, AV Joglekar, D Gray, ML Kaufman, M Ho, Z Romero, ... MOLECULAR THERAPY 22, S291-S291, 2014 | | 2014 |
| Optimization and Characterization of Product Manufacturing for a Clinical Trial of Gene Therapy for Sickle Cell Disease F Urbinati, B Campo, J Wherley, S Geiger, ML Kaufman, AR Cooper, ... MOLECULAR THERAPY 22, S16-S16, 2014 | | 2014 |
| A Pre-Clinical Model Of Hematopoietic Stem Cell Based Immunotherapy For Cancer Utilizing The NY-ESO-1 T-Cell Receptor and sr39TK PET Reporter/Suicide Gene EH Gschweng, MN McCracken, T Chodon, RC Koya, ML Kaufman, M Ho, ... Blood, The Journal of the American Society of Hematology 122 (21), 2020-2020, 2013 | | 2013 |
| Enhancing the Efficiency of Zinc Finger Nuclease Delivery by Integrase-Defective Lentiviral Vectors Using Valproic Acid AV Joglekar, M Ho, L Stein, S Sanadiki, RP Hollis, DB Kohn MOLECULAR THERAPY 21, S190-S190, 2013 | | 2013 |
