| An Erythroid Enhancer of BCL11A Subject to Genetic Variation Determines Fetal Hemoglobin Level DE Bauer, SC Kamran, S Lessard, J Xu, Y Fujiwara, C Lin, Z Shao, ... Science 342 (6155), 253-257, 2013 | 728 | 2013 |
| Nuclease-mediated gene editing by homologous recombination of the human globin locus RA Voit, A Hendel, SM Pruett-Miller, MH Porteus Nucleic acids research 42 (2), 1365-1378, 2014 | 123 | 2014 |
| Generation of an HIV resistant T-cell line by targeted “stacking” of restriction factors RA Voit, MA McMahon, SL Sawyer, MH Porteus Molecular therapy 21 (4), 786-795, 2013 | 94 | 2013 |
| SAPTA: a new design tool for improving TALE nuclease activity Y Lin, EJ Fine, Z Zheng, CJ Antico, RA Voit, MH Porteus, TJ Cradick, ... Nucleic acids research 42 (6), e47-e47, 2014 | 70 | 2014 |
| Stabilizing HIF to ameliorate anemia RA Voit, VG Sankaran Cell 180 (1), 6, 2020 | 49 | 2020 |
| Non-disruptive gene targeting MA Kay, M Porteus, J Barker, J Checketts, R Voit, A Barzel US Patent App. 13/838,927, 2013 | 38 | 2013 |
| A genetic disorder reveals a hematopoietic stem cell regulatory network co-opted in leukemia RA Voit, L Tao, F Yu, LD Cato, B Cohen, TJ Fleming, M Antoszewski, ... Nature Immunology 24 (1), 69-83, 2023 | 36 | 2023 |
| A unified model of human hemoglobin switching through single-cell genome editing Y Shen, JM Verboon, Y Zhang, N Liu, YJ Kim, S Marglous, ... Nature communications 12 (1), 4991, 2021 | 28 | 2021 |
| Familial thrombocytopenia due to a complex structural variant resulting in a WAC-ANKRD26 fusion transcript L Wahlster, JM Verboon, LS Ludwig, SC Black, W Luo, K Garg, RA Voit, ... Journal of Experimental Medicine 218 (6), e20210444, 2021 | 26 | 2021 |
| CD11c regulates hematopoietic stem and progenitor cells under stress L Hou, RA Voit, VG Sankaran, TA Springer, K Yuki Blood advances 4 (24), 6086-6097, 2020 | 21 | 2020 |
| Pathogenic BCL11A variants provide insights into the mechanisms of human fetal hemoglobin silencing Y Shen, R Li, K Teichert, KE Montbleau, JM Verboon, RA Voit, ... PLoS Genetics 17 (10), e1009835, 2021 | 15 | 2021 |
| CD11c regulates neutrophil maturation L Hou, RA Voit, M Shibamura-Fujiogi, S Koutsogiannaki, Y Li, Y Chen, ... Blood advances 7 (7), 1312-1325, 2023 | 14 | 2023 |
| MECOM deficiency: from bone marrow failure to impaired B-cell development RA Voit, VG Sankaran Journal of Clinical Immunology 43 (6), 1052-1066, 2023 | 10 | 2023 |
| Regulated expression of GATA1 as a gene therapy cure for Diamond-Blackfan anemia RA Voit, X Liao, B Cohen, M Armant, E Kamal, MM Huang, W Clarke, ... Blood 140 (Supplement 1), 986-987, 2022 | 8 | 2022 |
| Regulated GATA1 expression as a universal gene therapy for Diamond-Blackfan anemia RA Voit, X Liao, A Caulier, M Antoszewski, B Cohen, M Armant, HY Lu, ... Cell stem cell 32 (1), 38-52. e6, 2025 | 2 | 2025 |
| Gene therapy for congenital marrow failure syndromes–no longer grasping at straws? RA Voit, SJ Corey Haematologica 108 (11), 2880, 2023 | 2 | 2023 |
| Sowing the Seeds of Clonal Hematopoiesis LA Liggett, RA Voit, VG Sankaran Cell Stem Cell 27 (2), 195-197, 2020 | 2 | 2020 |
| Non-disruptive gene targeting MA Kay, M Porteus, J Barker, J Checketts, R Voit, A Barzel US Patent App. 15/457,923, 2017 | 2 | 2017 |
| Fine-Mapping and Genome Editing Reveal An Essential Erythroid Enhancer At The HbF-Associated BCL11A Locus DE Bauer, SC Kamran, S Lessard, J Xu, Y Fujiwara, C Lin, Z Shao, ... Blood 122 (21), 437, 2013 | 2 | 2013 |
| Nuclease mediated targeted genome modification in mammalian cells JC Barker, RA Voit, MH Porteus Site-directed insertion of transgenes, 327-352, 2013 | 2 | 2013 |
