From computational models of the splicing code to regulatory mechanisms and therapeutic implications

C Capitanchik, OG Wilkins, N Wagner… - Nature Reviews …, 2024 - nature.com
Since the discovery of RNA splicing and its role in gene expression, researchers have
sought a set of rules, an algorithm or a computational model that could predict the splice …

[HTML][HTML] mRNA vaccine sequence and structure design and optimization: Advances and challenges

L **, Y Zhou, S Zhang, SJ Chen - Journal of Biological Chemistry, 2024 - Elsevier
Messenger RNA (mRNA) vaccines have emerged as a powerful tool against communicable
diseases and cancers, as demonstrated by their huge success during the coronavirus …

gRNAde: Geometric Deep Learning for 3D RNA inverse design

CK Joshi, AR Jamasb, R Viñas, C Harris, S Mathis… - …, 2024 - pmc.ncbi.nlm.nih.gov
Computational RNA design tasks are often posed as inverse problems, where sequences
are designed based on adopting a single desired secondary structure without considering …

Rna-frameflow for de novo 3d rna backbone design

R Anand, CK Joshi, A Morehead… - ICML 2024 Workshop …, 2024 - openreview.net
We introduce RNA-FrameFlow, the first generative model for 3D RNA backbone design. We
build upon $ SE (3) $ flow matching for protein backbone generation and focus on …

Consistent features observed in structural probing data of eukaryotic RNAs

K Yamamura, K Asai, J Iwakiri - NAR Genomics and …, 2025 - academic.oup.com
Understanding RNA structure is crucial for elucidating its regulatory mechanisms. With the
recent commercialization of messenger RNA vaccines, the profound impact of RNA structure …

RNA-FrameFlow: Flow Matching for de novo 3D RNA Backbone Design

R Anand, CK Joshi, A Morehead, AR Jamasb… - arxiv preprint arxiv …, 2024 - arxiv.org
We introduce RNA-FrameFlow, the first generative model for 3D RNA backbone design. We
build upon SE (3) flow matching for protein backbone generation and establish protocols for …

[HTML][HTML] OpenASO: RNA Rescue—designing splice-modulating antisense oligonucleotides through community science

V Tse, M Guiterrez, J Townley, J Romano, J Pearl… - …, 2024 - pmc.ncbi.nlm.nih.gov
Splice-modulating antisense oligonucleotides (ASOs) are precision RNA-based drugs that
are becoming an established modality to treat human disease. Previously, we reported the …

A generative framework for enhanced cell-type specificity in rationally designed mRNAs

MS Khoroshkin, A Zinkevich, E Aristova, H Yousefi… - bioRxiv, 2024 - biorxiv.org
mRNA delivery offers new opportunities for disease treatment by directing cells to produce
therapeutic proteins. However, designing highly stable mRNAs with programmable cell type …