Epigenetics and human disease

HY Zoghbi, AL Beaudet - Cold Spring Harbor …, 2016 - cshperspectives.cshlp.org
Genetic causes for human disorders are being discovered at an unprecedented pace. A
growing subclass of disease-causing mutations involves changes in the epigenome or in the …

The intertwining of transposable elements and non-coding RNAs

M Hadjiargyrou, N Delihas - International journal of molecular sciences, 2013 - mdpi.com
Growing evidence shows a close association of transposable elements (TE) with non-coding
RNAs (ncRNA), and a significant number of small ncRNAs originate from TEs. Further …

Recurrent DUX4 fusions in B cell acute lymphoblastic leukemia of adolescents and young adults

T Yasuda, S Tsuzuki, M Kawazu, F Hayakawa… - Nature …, 2016 - nature.com
The oncogenic mechanisms underlying acute lymphoblastic leukemia (ALL) in adolescents
and young adults (AYA; 15–39 years old) remain largely elusive,,. Here we have searched …

A long ncRNA links copy number variation to a polycomb/trithorax epigenetic switch in FSHD muscular dystrophy

DS Cabianca, V Casa, B Bodega, A Xynos, E Ginelli… - Cell, 2012 - cell.com
Repetitive sequences account for more than 50% of the human genome.
Facioscapulohumeral muscular dystrophy (FSHD) is an autosomal-dominant disease …

The Tug1 lncRNA locus is essential for male fertility

JP Lewandowski, G Dumbović, AR Watson, T Hwang… - Genome biology, 2020 - Springer
Abstract Background Several long noncoding RNAs (lncRNAs) have been shown to function
as components of molecular machines that play fundamental roles in biology. While the …

Facioscapulohumeral muscular dystrophy family studies of DUX4 expression: evidence for disease modifiers and a quantitative model of pathogenesis

TI Jones, JCJ Chen, F Rahimov… - Human molecular …, 2012 - academic.oup.com
Facioscapulohumeral muscular dystrophy (FSHD), the most prevalent myopathy afflicting
both children and adults, is predominantly associated with contractions in the 4q35-localized …

A human pluripotent stem cell model of facioscapulohumeral muscular dystrophy-affected skeletal muscles

L Caron, D Kher, KL Lee, R McKernan… - Stem Cells …, 2016 - academic.oup.com
Facioscapulohumeral muscular dystrophy (FSHD) represents a major unmet clinical need
arising from the progressive weakness and atrophy of skeletal muscles. The dearth of …

Roles for long non-coding RNAs in physiology and disease

MT Melissari, P Grote - Pflügers Archiv-European Journal of Physiology, 2016 - Springer
While the vast majority of the genome is transcribed into RNA, only a small fraction of these
transcripts have protein-coding potential. A large fraction of the transcribed RNA belongs to …

DUX4-induced constitutive DNA damage and oxidative stress contribute to aberrant differentiation of myoblasts from FSHD patients

P Dmitriev, YB Saada, C Dib, E Ansseau… - Free Radical Biology …, 2016 - Elsevier
Facioscapulohumeral dystrophy (FSHD) is one of the three most common muscular
dystrophies in the Western world, however, its etiology remains only partially understood …

Diagnostic approach for FSHD revisited: SMCHD1 mutations cause FSHD2 and act as modifiers of disease severity in FSHD1

M Larsen, S Rost, N El Hajj, A Ferbert… - European Journal of …, 2015 - nature.com
Facioscapulohumeral muscular dystrophy (FSHD) is an autosomal dominant muscular
disorder with a wide clinical variability. Contractions of the D4Z4 macrosatellite repeat on …