Biodistribution, clearance, and long‐term fate of clinically relevant nanomaterials

J Bourquin, A Milosevic, D Hauser, R Lehner… - Advanced …, 2018 - Wiley Online Library
Realization of the immense potential of nanomaterials for biomedical applications will
require a thorough understanding of how they interact with cells, tissues, and organs. There …

Drug development for neurodevelopmental disorders: lessons learned from fragile X syndrome

EM Berry-Kravis, L Lindemann, AE Jønch… - Nature reviews Drug …, 2018 - nature.com
Neurodevelopmental disorders such as fragile X syndrome (FXS) result in lifelong cognitive
and behavioural deficits and represent a major public health burden. FXS is the most …

Modeling fragile X syndrome in the Fmr1 knockout mouse

TM Kazdoba, PT Leach, JL Silverman… - Intractable & rare …, 2014 - jstage.jst.go.jp
Summary Fragile X Syndrome (FXS) is a commonly inherited form of intellectual disability
and one of the leading genetic causes for autism spectrum disorder. Clinical symptoms of …

Evaluation of an activities of daily living scale for adolescents and adults with developmental disabilities

MJ Maenner, LE Smith, J Hong, R Makuch… - Disability and Health …, 2013 - Elsevier
BACKGROUND: Activity limitations are an important and useful dimension of disability, but
there are few validated measures of activity limitations for adolescents and adults with …

Updated report on tools to measure outcomes of clinical trials in fragile X syndrome

DB Budimirovic, E Berry-Kravis, CA Erickson… - Journal of …, 2017 - Springer
Abstract Objective Fragile X syndrome (FXS) has been the neurodevelopmental disorder
with the most active translation of preclinical breakthroughs into clinical trials. This process …

The fragile X syndrome–autism comorbidity: what do we really know?

L Abbeduto, A McDuffie, AJ Thurman - Frontiers in genetics, 2014 - frontiersin.org
Autism spectrum disorder (ASD) is a common comorbid condition in people with fragile X
syndrome (FXS). It has been assumed that ASD symptoms reflect the same underlying …

Improving IQ measurement in intellectual disabilities using true deviation from population norms

SM Sansone, A Schneider, E Bickel… - Journal of …, 2014 - Springer
Background Intellectual disability (ID) is characterized by global cognitive deficits, yet the
very IQ tests used to assess ID have limited range and precision in this population …

The NIH Toolbox Cognitive Battery for intellectual disabilities: three preliminary studies and future directions

D Hessl, SM Sansone, E Berry-Kravis, K Riley… - Journal of …, 2016 - Springer
Background Recent advances in understanding molecular and synaptic mechanisms of
intellectual disabilities (ID) in fragile X syndrome (FXS) and Down syndrome (DS) through …

Current opinions on the present and future use of functional near-infrared spectroscopy in psychiatry

R Li, H Hosseini, M Saggar, SC Balters… - …, 2023 - spiedigitallibrary.org
Functional near-infrared spectroscopy (fNIRS) is an optical imaging technique for assessing
human brain activity by noninvasively measuring the fluctuation of cerebral oxygenated-and …

A neurodevelopmental survey of Angelman syndrome with genotype-phenotype correlations

JK Gentile, WH Tan, LT Horowitz… - … of Developmental & …, 2010 - journals.lww.com
Objective: Angelman syndrome (AS) is a neurodevelopmental disorder caused by a deletion
on chromosome 15, uniparental disomy, imprinting defect, or UBE3A mutation. It is …