Sickle cell disease: a global patient registry review
O Borecka, A Ofori, F Amini, S Llewellyn - Future Rare Diseases, 2022 - Taylor & Francis
Sickle cell disease (SCD) is one of the most common inherited diseases. This review
identified and assessed key characteristics of the increasing number of SCD registries …
identified and assessed key characteristics of the increasing number of SCD registries …
Patient-reported impact of Charcot-Marie-Tooth disease: protocol for a real-world digital lifestyle study
Charcot-Marie-Tooth disease (CMT) is a rare, chronic, progressive motor and sensory
neuropathy affecting the peripheral nervous system. This study will explore the real-world …
neuropathy affecting the peripheral nervous system. This study will explore the real-world …
[PDF][PDF] The patient-reported impact of Charcot-Marie-Tooth disease in the real world: the design and conduct of a digital lifestyle study (CMT&Me)
Background Charcot-Marie-Tooth disease (CMT) is a rare, chronic, progressive motor and
sensory neuropathy that affects the peripheral nervous system, leading to progressive …
sensory neuropathy that affects the peripheral nervous system, leading to progressive …