[HTML][HTML] Medium-chain acyl-coenzyme A dehydrogenase deficiency

IJ Chang, C Lam, J Vockley - GeneReviews®[Internet], 2024‏ - ncbi.nlm.nih.gov
Medium-chain acyl-coenzyme A dehydrogenase (MCAD) is one of the enzymes involved in
mitochondrial fatty acid β-oxidation. Fatty acid β-oxidation fuels hepatic ketogenesis, which …

Experiences of perinatal genetic screening for people from migrant and refugee backgrounds: a sco** review

A Kanga-Parabia, AD Archibald, LJ Biggs… - European Journal of …, 2025‏ - nature.com
People from refugee and migrant backgrounds often face poor experiences and outcomes in
healthcare, and genetic healthcare is no exception. Understanding whether and how these …

Performance of single‐gene noninvasive prenatal testing for autosomal recessive conditions in a general population setting

J Wynn, J Hoskovec, RD Carter, MJ Ross… - Prenatal …, 2023‏ - Wiley Online Library
Objective Carrier screening with reflex to single‐gene noninvasive prenatal testing (sgNIPT)
is an alternative approach for identifying pregnancies at risk for inherited autosomal …

Bridging the Gap: Animal Models in Next-Generation Reproductive Technologies for Male Fertility Preservation

PM Aponte, MA Gutierrez-Reinoso, M Garcia-Herreros - Life, 2023‏ - mdpi.com
This review aims to explore advanced reproductive technologies for male fertility
preservation, underscoring the essential role that animal models have played in sha** …

Consensus guidelines for the diagnosis and management of succinic semialdehyde dehydrogenase deficiency

IT Latzer, M Bertoldi, N Blau, ML DiBacco… - Molecular Genetics and …, 2024‏ - Elsevier
Succinic semialdehyde dehydrogenase deficiency (SSADHD)(OMIM# 271980) is a rare
autosomal recessive metabolic disorder caused by pathogenic variants of ALDH5A1 …

Survey of the Landscape of Society Practice Guidelines for Genetic Testing of Neurodevelopmental Disorders

S Srivastava, JJ Cole, JS Cohen, M Chopra… - Annals of …, 2024‏ - Wiley Online Library
Genetic testing of patients with neurodevelopmental disabilities (NDDs) is critical for
diagnosis, medical management, and access to precision therapies. Because genetic …

Population-based genetic carrier screening. A consensus statement from the Spanish societies: AEGH, AEDP, ASEBIR, SEAGEN, SEF and SEGCD

X Vendrell, A Abulí, C Serra, JJ Guillén… - European Journal of …, 2024‏ - nature.com
Autosomal recessive or X-linked disorders are passed from parents to offspring through
Mendelian inheritance patterns and may lead to severe clinical manifestations in early …

Embryo and Fetal Gene Editing: Technical Challenges and Progress towards Clinical Applications

CNZ Mattar, WL Chew, P San Lai - Molecular Therapy Methods & Clinical …, 2024‏ - cell.com
Gene modification therapies (GMT) are slowly but steadily making progress towards clinical
application. As the majority of rare diseases have an identified genetic cause, and as rare …

Reproductive Carrier Screening: Identifying Families at Risk for Familial Hypercholesterolemia in the United States

V Souter, E Becraft, S Brummitt, BJ Gall… - Circulation: Genomic …, 2024‏ - Am Heart Assoc
BACKGROUND: Familial hypercholesterolemia is a treatable genetic condition but remains
underdiagnosed. We reviewed the frequency of pathogenic or likely pathogenic (P/LP) …

Update to the essential genomic nursing competencies and outcome indicators

KA Calzone, L Stokes, C Peterson… - Journal of Nursing …, 2024‏ - Wiley Online Library
Introduction Genomic healthcare applications have relevance to all healthcare professionals
including nursing, and most evidence‐based clinical applications impact the quality and …