[HTML][HTML] CRISPR/Cas9 platforms for genome editing in plants: developments and applications

X Ma, Q Zhu, Y Chen, YG Liu - Molecular plant, 2016 - cell.com
The clustered regularly interspaced short palindromic repeat (CRISPR)-associated protein9
(Cas9) genome editing system (CRISPR/Cas9) is adapted from the prokaryotic type II …

Methods for optimizing CRISPR-Cas9 genome editing specificity

J Tycko, VE Myer, PD Hsu - Molecular cell, 2016 - cell.com
Advances in the development of delivery, repair, and specificity strategies for the CRISPR-
Cas9 genome engineering toolbox are hel** researchers understand gene function with …

TGF-β inhibition via CRISPR promotes the long-term efficacy of CAR T cells against solid tumors

N Tang, C Cheng, X Zhang, M Qiao, N Li, W Mu… - JCI …, 2020 - pmc.ncbi.nlm.nih.gov
In recent years, chimeric antigen receptor–modified T cell (CAR T cell) therapy has proven to
be a promising approach against cancer. Nonetheless, this approach still faces multiple …

Increasing the specificity of CRISPR systems with engineered RNA secondary structures

DD Kocak, EA Josephs, V Bhandarkar, SS Adkar… - Nature …, 2019 - nature.com
CRISPR (clustered regularly interspaced short palindromic repeat) systems have been
broadly adopted for basic science, biotechnology, and gene and cell therapy. In some …

Pooled CRISPR screening with single-cell transcriptome readout

P Datlinger, AF Rendeiro, C Schmidl, T Krausgruber… - Nature …, 2017 - nature.com
CRISPR-based genetic screens are accelerating biological discovery, but current methods
have inherent limitations. Widely used pooled screens are restricted to simple readouts …

In vivo genome editing improves muscle function in a mouse model of Duchenne muscular dystrophy

CE Nelson, CH Hakim, DG Ousterout, PI Thakore… - Science, 2016 - science.org
Duchenne muscular dystrophy (DMD) is a devastating disease affecting about 1 out of 5000
male births and caused by mutations in the dystrophin gene. Genome editing has the …

Non‐viral CRISPR/Cas gene editing in vitro and in vivo enabled by synthetic nanoparticle co‐delivery of Cas9 mRNA and sgRNA

JB Miller, S Zhang, P Kos, H **ong, K Zhou… - Angewandte …, 2017 - Wiley Online Library
CRISPR/Cas is a revolutionary gene editing technology with wide‐ranging utility. The safe,
non‐viral delivery of CRISPR/Cas components would greatly improve future therapeutic …

Modeling colorectal cancer using CRISPR-Cas9–mediated engineering of human intestinal organoids

M Matano, S Date, M Shimokawa, A Takano, M Fujii… - Nature medicine, 2015 - nature.com
Human colorectal tumors bear recurrent mutations in genes encoding proteins operative in
the WNT, MAPK, TGF-β, TP53 and PI3K pathways,. Although these pathways influence …

Cationic lipid-mediated delivery of proteins enables efficient protein-based genome editing in vitro and in vivo

JA Zuris, DB Thompson, Y Shu, JP Guilinger… - Nature …, 2015 - nature.com
Efficient intracellular delivery of proteins is needed to fully realize the potential of protein
therapeutics. Current methods of protein delivery commonly suffer from low tolerance for …

Genome engineering using the CRISPR-Cas9 system

FA Ran, PD Hsu, J Wright, V Agarwala, DA Scott… - Nature protocols, 2013 - nature.com
Targeted nucleases are powerful tools for mediating genome alteration with high precision.
The RNA-guided Cas9 nuclease from the microbial clustered regularly interspaced short …