Fedratinib in myelofibrosis

A Mullally, J Hood, C Harrison, R Mesa - Blood advances, 2020 - ashpublications.org
Following the discovery of the JAK2V617F mutation in myeloproliferative neoplasms in
2005, fedratinib was developed as a small molecular inhibitor of JAK2. It was optimized to …

Age-Associated TET2 Mutations: Common Drivers of Myeloid Dysfunction, Cancer and Cardiovascular Disease

CK Ferrone, M Blydt-Hansen, MJ Rauh - International journal of molecular …, 2020 - mdpi.com
Acquired, inactivating mutations in Tet methylcytosine dioxygenase 2 (TET2) are detected in
peripheral blood cells of a remarkable 5%–10% of adults greater than 65 years of age. They …

Ruxolitinib versus best available therapy for polycythemia vera intolerant or resistant to hydroxycarbamide in a randomized trial

CN Harrison, J Nangalia, R Boucher… - Journal of Clinical …, 2023 - ascopubs.org
PURPOSE Polycythemia vera (PV) is characterized by JAK/STAT activation, thrombotic/
hemorrhagic events, systemic symptoms, and disease transformation. In high-risk PV …

Ropeginterferon alfa-2b versus phlebotomy in low-risk patients with polycythaemia vera (Low-PV study): a multicentre, randomised phase 2 trial

T Barbui, AM Vannucchi, V De Stefano… - The Lancet …, 2021 - thelancet.com
Background There is no evidence that phlebotomy alone is sufficient to steadily maintain
haematocrit on target level in low-risk patients with polycythaemia vera. This study aimed to …

Reversal of malignant ADAR1 splice isoform switching with Rebecsinib

LA Crews, W Ma, L Ladel, J Pham, L Balaian, SK Steel… - Cell Stem Cell, 2023 - cell.com
Adenosine deaminase acting on RNA1 (ADAR1) preserves genomic integrity by preventing
retroviral integration and retrotransposition during stress responses. However, inflammatory …

Survival in hematological malignancies in the Nordic countries through a half century with correlation to treatment

K Hemminki, J Hemminki, A Försti, A Sud - Leukemia, 2023 - nature.com
Studies of survival in hematological malignancies (HMs) have generally shown an
improvement over time, although most of these studies are limited by a short follow-up …

Long‐term pharmacodynamic and clinical effects of twice‐versus once‐daily low‐dose aspirin in essential thrombocythemia: The ARES trial

B Rocca, A Tosetto, G Petrucci, E Rossi… - American Journal of …, 2024 - Wiley Online Library
Patients with essential thrombocythemia (ET) are treated with once‐daily low‐dose aspirin
to prevent thrombosis, but their accelerated platelet turnover shortens the antiplatelet effect …

Next generation therapeutics for the treatment of myelofibrosis

D Tremblay, J Mascarenhas - Cells, 2021 - mdpi.com
Myelofibrosis is a myeloproliferative neoplasm characterized by splenomegaly,
constitutional symptoms, bone marrow fibrosis, and a propensity towards transformation to …

Validation of the IPSET score for thrombosis in patients with prefibrotic myelofibrosis

P Guglielmelli, A Carobbio, E Rumi, V De Stefano… - Blood cancer …, 2020 - nature.com
Pre-fibrotic myelofibrosis (pre-PMF) and essential thrombocythemia (ET) are characterized
by similarly increased rate of thrombotic events, but no study specifically analyzed risk …

Current management strategies for polycythemia vera and essential thrombocythemia

P Guglielmelli, AM Vannucchi - Blood Reviews, 2020 - Elsevier
Polycythemia vera (PV) and essential thrombocythemia (ET) are myeloproliferative
neoplasms characterized by increased rate of cardiovascular events, a varying burden of …