Challenges in treating Charcot-Marie-Tooth disease and related neuropathies: current management and future perspectives

C Pisciotta, P Saveri, D Pareyson - Brain sciences, 2021 - mdpi.com
There is still no effective drug treatment available for Charcot-Marie-Tooth neuropathies
(CMT). Current management relies on rehabilitation therapy, surgery for skeletal deformities …

Hereditary neuropathy

C Pisciotta, ME Shy - Handbook of clinical neurology, 2023 - Elsevier
The hereditary neuropathies, collectively referred as Charcot–Marie–Tooth disease (CMT)
and related disorders, are heterogeneous genetic peripheral nerve disorders that …

Triggers and alleviating factors for fatigue in Parkinson's disease

I Lin, B Edison, S Mantri, S Albert, M Daeschler… - PLoS …, 2021 - journals.plos.org
Background Fatigue is common in Parkinson's Disease, but few effective treatments are
available for it. Exploring triggers and alleviating factors, including effects of exercise, could …

Frequency, entity and determinants of fatigue in Charcot–Marie–Tooth disease

M Bellofatto, A Bertini, I Tramacere… - European Journal of …, 2023 - Wiley Online Library
Background and purpose Fatigue, a disabling symptom in many neuromuscular disorders,
has been reported also in Charcot–Marie–Tooth disease (CMT). The presence of fatigue …

Neuromuscular junction involvement in inherited motor neuropathies: genetic heterogeneity and effect of oral salbutamol treatment

G McMacken, RG Whittaker, R Wake, H Lochmuller… - Journal of …, 2023 - Springer
Objectives Inherited defects of the neuromuscular junction (NMJ) comprise an increasingly
diverse range of diseases. Several recently identified genes highlight the overlap between …

Pharmacological doses of thiamine benefit patients with the charcot–marie–tooth neuropathy by changing thiamine diphosphate levels and affecting regulation of …

AV Artiukhov, ON Solovjeva, NV Balashova… - Biochemistry …, 2024 - Springer
Abstract Charcot–Marie–Tooth (CMT) neuropathy is a polygenic disorder of peripheral
nerves with no effective cure. Thiamine (vitamin B1) is a neurotropic compound that …

Exploratory study of physical activity in persons with Charcot-Marie-Tooth disease

E Anens, M Emtner, K Hellström - Archives of Physical Medicine and …, 2015 - Elsevier
Objectives To explore and describe the perceived facilitators and barriers to physical activity,
and to examine the physical activity correlates in people with Charcot-Marie-Tooth (CMT) …

Exploring quality of life in people with slowly-progressive neuromuscular disease

A Dany, A Rapin, C Réveillère, A Calmus… - Disability and …, 2017 - Taylor & Francis
Purpose: A qualitative work is conducted to enable later the construction of a health-related
quality of life (HRQL) questionnaire for patients with slowly-progressive neuromuscular …

Therapeutic options in Charcot–Marie–Tooth diseases

S Mathis, L Magy, JM Vallat - Expert review of neurotherapeutics, 2015 - Taylor & Francis
Charcot–Marie–Tooth (CMT) diseases represent a heterogeneous genetic disorder (more
than 80 genes are implicated in these inherited neuropathies), but sharing a similar …

Review of general and head and neck/oral and maxillofacial features of Charcot-Marie-Tooth disease and dental management considerations

JK Brooks, NC Porter, KA Bisordi, CE Miclat… - Oral Surgery, Oral …, 2022 - Elsevier
Charcot-Marie-Tooth disease (CMTD) is an uncommon progressive neuromuscular disorder
of the peripheral nervous system and primarily leads to distal extremity weakness and …