CRISPR technologies for genome, epigenome and transcriptome editing

L Villiger, J Joung, L Koblan, J Weissman… - … Reviews Molecular Cell …, 2024 - nature.com
Our ability to edit genomes lags behind our capacity to sequence them, but the growing
understanding of CRISPR biology and its application to genome, epigenome and …

Structural basis for the activation of a compact CRISPR-Cas13 nuclease

X Deng, E Osikpa, J Yang, SJ Oladeji, J Smith… - Nature …, 2023 - nature.com
The CRISPR-Cas13 ribonucleases have been widely applied for RNA knockdown and
transcriptional modulation owing to their high programmability and specificity. However, the …

Next-generation CRISPR technology for genome, epigenome and mitochondrial editing

CH Lau, QL Liang, H Zhu - Transgenic Research, 2024 - Springer
The application of rapidly growing CRISPR toolboxes and methods has great potential to
transform biomedical research. Here, we provide a snapshot of up-to-date CRISPR …

A strategy for Cas13 miniaturization based on the structure and AlphaFold

F Zhao, T Zhang, X Sun, X Zhang, L Chen… - Nature …, 2023 - nature.com
The small size of the Cas nuclease fused with various effector domains enables a broad
range of function. Although there are several ways of reducing the size of the Cas nuclease …

Characterization of RNA editing and gene therapy with a compact CRISPR-Cas13 in the retina

S Kumar, YW Hsiao, VHY Wong, D Aubin… - Proceedings of the …, 2024 - pnas.org
CRISPR-Cas13 nucleases are programmable RNA-targeting effectors that can silence gene
expression in a transient manner. Recent iterations of Cas13 nucleases are compact for …

Insights gained from RNA editing targeted by the CRISPR-Cas13 family

L Liu, DS Pei - International Journal of Molecular Sciences, 2022 - mdpi.com
Clustered regularly interspaced short palindromic repeat (CRISPR)/CRISPR-associated
protein (Cas) systems, especially type II (Cas9) systems, have been widely developed for …

AAV-mediated gene therapies by miniature gene editing tools

X Kong, T Li, H Yang - Science China Life Sciences, 2024 - Springer
The advent of CRISPR-Cas has revolutionized precise gene editing. While pioneering
CRISPR nucleases like Cas9 and Cas12 generate targeted DNA double-strand breaks …

[PDF][PDF] CRISPR-Cas target recognition for sensing viral and cancer biomarkers

S Rahimi, SR Balusamy, H Perumalsamy… - Nucleic acids …, 2024 - academic.oup.com
Nucleic acid-based diagnostics is a promising venue for detection of pathogens causing
infectious diseases and mutations related to cancer. However, this type of diagnostics still …

Genome and transcriptome engineering by compact and versatile CRISPR-Cas systems

G Aquino-Jarquin - Drug Discovery Today, 2023 - Elsevier
Comparative genomics has enabled the discovery of tiny clustered regularly interspaced
short palindromic repeat (CRISPR) bacterial immune system effectors with enormous …

Enhanced RNA knockdown efficiency with engineered fusion guide RNAs that function with both CRISPR-CasRx and hammerhead ribozyme

Y Zhan, C Cao, A Li, H Mei, Y Liu - Genome Biology, 2023 - Springer
Background CRISPR-Cas13 is a newly emerging RNA knockdown technology that is
comparable to RNAi. Among all members of Cas13, CasRx degrades RNA in human cells …