The growth of siRNA-based therapeutics: Updated clinical studies

MM Zhang, R Bahal, TP Rasmussen… - Biochemical …, 2021 - Elsevier
More than two decades after the natural gene-silencing mechanism of RNA interference was
elucidated, small interfering RNA (siRNA)-based therapeutics have finally broken into the …

Inherited retinal diseases: linking genes, disease-causing variants, and relevant therapeutic modalities

N Schneider, Y Sundaresan, P Gopalakrishnan… - Progress in retinal and …, 2022 - Elsevier
Inherited retinal diseases (IRDs) are a clinically complex and heterogenous group of visual
impairment phenotypes caused by pathogenic variants in at least 277 nuclear and …

CRISPR interference (CRISPRi) for sequence-specific control of gene expression

MH Larson, LA Gilbert, X Wang, WA Lim… - Nature protocols, 2013 - nature.com
Sequence-specific control of gene expression on a genome-wide scale is an important
approach for understanding gene functions and for engineering genetic regulatory systems …

Programmable RNA recognition and cleavage by CRISPR/Cas9

MR O'Connell, BL Oakes, SH Sternberg… - Nature, 2014 - nature.com
The CRISPR-associated protein Cas9 is an RNA-guided DNA endonuclease that uses RNA–
DNA complementarity to identify target sites for sequence-specific double-stranded DNA …

Nanotechnological approaches in prostate cancer therapy: integration of engineering and biology

M Ashrafizadeh, S Aghamiri, SC Tan, A Zarrabi… - Nano Today, 2022 - Elsevier
Nanocarriers have received special attention in biomedicine for the treatment of various
diseases, especially cancer, as one of the leading causes of death worldwide. Nanocarriers …

The implication of long non-coding RNAs in the diagnosis, pathogenesis and drug resistance of pancreatic ductal adenocarcinoma and their possible therapeutic …

G Pandya, A Kirtonia, G Sethi, AK Pandey… - Biochimica et Biophysica …, 2020 - Elsevier
Pancreatic ductal adenocarcinoma (PDAC) is one of the lethal malignancies with the lowest
median and overall survival rate among all human malignancies. The major problems with …

Pullulan: A novel molecule for biomedical applications

RS Singh, N Kaur, V Rana, JF Kennedy - Carbohydrate polymers, 2017 - Elsevier
Pullulan is an imperative natural polymer produced commercially by yeast like fungus
Aureobasidium pullulans. It is non-toxic, non-immunogenic, non-carcinogenic and non …

Pullulan and pullulan derivatives as promising biomolecules for drug and gene targeting

RS Singh, N Kaur, JF Kennedy - Carbohydrate Polymers, 2015 - Elsevier
Pullulan is a water soluble exo-polysaccharide produced by yeast like fungus
Aureobasidium pullulans. Pullulan structure have a unique characteristic ie co-existence of …

Fungal exopolysaccharides: Properties, sources, modifications, and biomedical applications

M Hamidi, OV Okoro, PB Milan, MR Khalili… - Carbohydrate …, 2022 - Elsevier
Fungal exopolysaccharides (EPSs) are natural biopolymers with diverse potential
applications in the biomedical, packaging, cosmetic, and food industries. Fungal EPSs are …

Generating single cell–derived knockout clones in mammalian cells with CRISPR/Cas9

CJ Giuliano, A Lin, V Girish… - Current protocols in …, 2019 - Wiley Online Library
CRISPR/Cas9 technology enables the rapid generation of loss‐of‐function mutations in a
targeted gene in mammalian cells. A single cell harboring those mutations can be used to …