Promoting the clearance of neurotoxic proteins in neurodegenerative disorders of ageing

B Boland, WH Yu, O Corti, B Mollereau… - Nature reviews Drug …, 2018 - nature.com
Neurodegenerative disorders of ageing (NDAs) such as Alzheimer disease, Parkinson
disease, frontotemporal dementia, Huntington disease and amyotrophic lateral sclerosis …

Stress granules, RNA-binding proteins and polyglutamine diseases: too much aggregation?

A Marcelo, R Koppenol, LP de Almeida, CA Matos… - Cell death & …, 2021 - nature.com
Stress granules (SGs) are membraneless cell compartments formed in response to different
stress stimuli, wherein translation factors, mRNAs, RNA-binding proteins (RBPs) and other …

Autophagy induction as a therapeutic strategy for neurodegenerative diseases

A Djajadikerta, S Keshri, M Pavel, R Prestil… - Journal of molecular …, 2020 - Elsevier
Autophagy is a major, conserved cellular pathway by which cells deliver cytoplasmic
contents to lysosomes for degradation. Genetic studies have revealed extensive links …

PINK1 and BECN1 relocalize at mitochondria-associated membranes during mitophagy and promote ER-mitochondria tethering and autophagosome formation

V Gelmetti, P De Rosa, L Torosantucci, ES Marini… - Autophagy, 2017 - Taylor & Francis
Mitophagy is a highly specialized process to remove dysfunctional or superfluous
mitochondria through the macroautophagy/autophagy pathway, aimed at protecting cells …

Mutation in ATG5 reduces autophagy and leads to ataxia with developmental delay

M Kim, E Sandford, D Gatica, Y Qiu, X Liu, Y Zheng… - elife, 2016 - elifesciences.org
Autophagy is required for the homeostasis of cellular material and is proposed to be
involved in many aspects of health. Defects in the autophagy pathway have been observed …

Oligonucleotide therapy mitigates disease in spinocerebellar ataxia type 3 mice

HS McLoughlin, LR Moore, R Chopra… - Annals of …, 2018 - Wiley Online Library
Objective Spinocerebellar ataxia type 3 (SCA3), also known as Machado–Joseph disease,
is the most common dominantly inherited ataxia. Despite advances in understanding this …

Machado–Joseph disease/spinocerebellar ataxia type 3: lessons from disease pathogenesis and clues into therapy

CA Matos, LP de Almeida… - Journal of …, 2019 - Wiley Online Library
Abstract Machado–Joseph disease (MJD), also known as spinocerebellar ataxia type 3
(SCA 3), is an incurable disorder, widely regarded as the most common form of …

Autophagic and endo-lysosomal dysfunction in neurodegenerative disease

BR Malik, DC Maddison, GA Smith, OM Peters - Molecular brain, 2019 - Springer
Due to their post-mitotic state, metabolic demands and often large polarised morphology, the
function and survival of neurons is dependent on an efficient cellular waste clearance …

Clinical gene therapy for neurodegenerative diseases: past, present, and future

F Piguet, S Alves, N Cartier - Human gene therapy, 2017 - liebertpub.com
Clinical gene therapy has made important advances over the last decade. Among
neurological diseases, severe genetic neurodegenerative conditions have been the focus of …

Targeting autophagy in neurodegenerative diseases

RL Vidal, S Matus, L Bargsted, C Hetz - Trends in pharmacological …, 2014 - cell.com
The most prevalent neurodegenerative disorders involve protein misfolding and the
aggregation of specific proteins. Autophagy is becoming an attractive target to treat …