Phenotypic variability to medication management: an update on fragile X syndrome

NA Elhawary, IA AlJahdali, IS Abumansour, ZA Azher… - Human Genomics, 2023 - Springer
This review discusses the discovery, epidemiology, pathophysiology, genetic etiology,
molecular diagnosis, and medication-based management of fragile X syndrome (FXS). It …

Molecular pathogenesis and peripheral monitoring of adult fragile X-associated syndromes

LM Valor, JC Morales, I Hervás-Corpión… - International Journal of …, 2021 - mdpi.com
Abnormal trinucleotide expansions cause rare disorders that compromise quality of life and,
in some cases, lifespan. In particular, the expansions of the CGG-repeats stretch at the 5' …

A sensitive and reproducible qRT-PCR assay detects physiological relevant trace levels of FMR1 mRNA in individuals with Fragile X syndrome

D Straub, LM Schmitt, AE Boggs, PS Horn… - Scientific Reports, 2023 - nature.com
Fragile X syndrome (FXS) is the most common inherited intellectual disability. FXS is caused
by a trinucleotide repeat expansion in the 5′ untranslated region of the FMR1 gene, which …

Variable expressivity in fragile X syndrome: towards the identification of molecular characteristics that modify the phenotype

C Payán-Gómez, J Ramirez-Cheyne… - The Application of …, 2021 - Taylor & Francis
Fragile X syndrome (FXS), is an X-linked inherited genetic disease. FXS is the leading
cause of inherited intellectual disability and autism in the world. Those affected are …

[HTML][HTML] Regulation of Bone Morphogenetic Protein Receptor Type II Expression by FMR1/Fragile X Mental Retardation Protein in Human Granulosa Cells in the …

XP Nguyen, A Vilkaite, U Bender, JE Dietrich… - International Journal of …, 2024 - mdpi.com
Fragile X mental retardation protein (FMRP) is a translational repressor encoded by FMR1. It
targets bone morphogenetic protein receptor type II (BMPR2), which regulates granulosa …

The Prognostic and Therapeutic Potential of Fragile X Mental Retardation 1 (FMR1) Gene Expression in Prostate Adenocarcinoma: Insights into Survival Outcomes …

S Baldi, B Amer, F Alnadari… - International …, 2024 - pmc.ncbi.nlm.nih.gov
Prostate adenocarcinoma (PRAD) is the second most common tumor associated with death.
The role and mechanisms of the fragile X mental retardation 1 (FMR1) gene in PRAD remain …

Position Effect Variegation: Role of the Local Chromatin Context in Gene Expression Regulation

LV Boldyreva, EN Andreyeva, AV Pindyurin - Molecular Biology, 2022 - Springer
Position effect variegation (PEV) is a phenomenon wherein the expression level of a gene
strongly depends on its genomic position. PEV can be observed when a gene is moved via …

[PDF][PDF] Некодирующие РНК в патогенезе заболеваний, ассоциированных с ломкой Х-хромосомой

ДВ Юдкин - vector.nsc.ru
На сегодняшний день существует целый ряд заболеваний, обобщенных под общим
термином «фраксопатии». Он включает в себя синдромы, связанные с экспансией CGG …