Induced pluripotent stem cell technology: a decade of progress

Y Shi, H Inoue, JC Wu, S Yamanaka - Nature reviews Drug discovery, 2017 - nature.com
Since the advent of induced pluripotent stem cell (iPSC) technology a decade ago,
enormous progress has been made in stem cell biology and regenerative medicine. Human …

Pluripotent stem cells in disease modelling and drug discovery

Y Avior, I Sagi, N Benvenisty - Nature reviews Molecular cell biology, 2016 - nature.com
Experimental modelling of human disorders enables the definition of the cellular and
molecular mechanisms underlying diseases and the development of therapies for treating …

HSP70 chaperones RNA-free TDP-43 into anisotropic intranuclear liquid spherical shells

H Yu, S Lu, K Gasior, D Singh, S Vazquez-Sanchez… - Science, 2021 - science.org
INTRODUCTION Aggregation of the RNA binding protein TDP-43 (TAR DNA-binding protein
43) is a common pathological hallmark shared by several age-related neurodegenerative …

[HTML][HTML] In silico labeling: predicting fluorescent labels in unlabeled images

EM Christiansen, SJ Yang, DM Ando, A Javaherian… - Cell, 2018 - cell.com
Microscopy is a central method in life sciences. Many popular methods, such as antibody
labeling, are used to add physical fluorescent labels to specific cellular constituents …

Modeling sporadic ALS in iPSC-derived motor neurons identifies a potential therapeutic agent

K Fujimori, M Ishikawa, A Otomo, N Atsuta… - Nature medicine, 2018 - nature.com
Amyotrophic lateral sclerosis (ALS) is a heterogeneous motor neuron disease for which no
effective treatment is available, despite decades of research into SOD1-mutant familial ALS …

Screening out irrelevant cell-based models of disease

P Horvath, N Aulner, M Bickle, AM Davies… - Nature reviews Drug …, 2016 - nature.com
The common and persistent failures to translate promising preclinical drug candidates into
clinical success highlight the limited effectiveness of disease models currently used in drug …

In vitro Models of Neurodegenerative Diseases

A Slanzi, G Iannoto, B Rossi, E Zenaro… - Frontiers in cell and …, 2020 - frontiersin.org
Neurodegenerative diseases are progressive degenerative conditions characterized by the
functional deterioration and ultimate loss of neurons. These incurable and debilitating …

Evaluating cell reprogramming, differentiation and conversion technologies in neuroscience

J Mertens, MC Marchetto, C Bardy… - Nature Reviews …, 2016 - nature.com
The scarcity of live human brain cells for experimental access has for a long time limited our
ability to study complex human neurological disorders and elucidate basic neuroscientific …

Small-molecule modulation of TDP-43 recruitment to stress granules prevents persistent TDP-43 accumulation in ALS/FTD

MY Fang, S Markmiller, AQ Vu, A Javaherian… - Neuron, 2019 - cell.com
Stress granules (SGs) form during cellular stress and are implicated in neurodegenerative
diseases such as amyotrophic lateral sclerosis and frontotemporal dementia (ALS/FTD). To …

Genetic predispositions of Parkinson's disease revealed in patient-derived brain cells

J Tran, H Anastacio, C Bardy - NPJ Parkinson's disease, 2020 - nature.com
Parkinson's disease (PD) is the second most prevalent neurological disorder and has been
the focus of intense investigations to understand its etiology and progression, but it still lacks …