[HTML][HTML] Polymer-and lipid-based nanocarriers for ocular drug delivery: current status and future perspectives

H Han, S Li, M Xu, Y Zhong, W Fan, J Xu, T Zhou… - Advanced Drug Delivery …, 2023 - Elsevier
Ocular diseases seriously affect patients' vision and life quality, with a global morbidity of
over 43 million blindness. However, efficient drug delivery to treat ocular diseases …

Structure and function of cationic and ionizable lipids for nucleic acid delivery

D Sun, ZR Lu - Pharmaceutical Research, 2023 - Springer
Hereditary genetic diseases, cancer, and infectious diseases are affecting global health and
become major health issues, but the treatment development remains challenging. Gene …

A biodegradable nanocapsule delivers a Cas9 ribonucleoprotein complex for in vivo genome editing

G Chen, AA Abdeen, Y Wang, PK Shahi… - Nature …, 2019 - nature.com
Delivery technologies for the CRISPR-Cas9 (CRISPR, clustered regularly interspaced short
palindromic repeats) gene editing system often require viral vectors, which pose safety …

Systemic delivery of tumor-targeting siRNA nanoparticles against an oncogenic LncRNA facilitates effective triple-negative breast cancer therapy

AM Vaidya, Z Sun, N Ayat, A Schilb, X Liu… - Bioconjugate …, 2019 - ACS Publications
Long noncoding RNAs (lncRNAs), by virtue of their versatility and multilevel gene regulation,
have emerged as attractive pharmacological targets for treating heterogeneous and …

Gene therapy for inherited retinal disease: Long-term durability of effect

BP Leroy, MD Fischer, JG Flannery, RE MacLaren… - Ophthalmic …, 2023 - karger.com
The recent approval of voretigene neparvovec (Luxturna®) for patients with biallelic RPE65
mutation-associated inherited retinal dystrophy with viable retinal cells represents an …

[HTML][HTML] Optimizing synthetic nucleic acid and protein nanocarriers: The chemical evolution approach

F Freitag, E Wagner - Advanced drug delivery reviews, 2021 - Elsevier
Optimizing synthetic nanocarriers is like searching for a needle in a haystack. How to find
the most suitable carrier for intracellular delivery of a specified macromolecular nanoagent …

A pH-responsive silica–metal–organic framework hybrid nanoparticle for the delivery of hydrophilic drugs, nucleic acids, and CRISPR-Cas9 genome-editing …

Y Wang, PK Shahi, R **e, H Zhang, AA Abdeen… - Journal of Controlled …, 2020 - Elsevier
Efficient delivery of hydrophilic drugs, nucleic acids, proteins, and any combination thereof is
essential for various biomedical applications. Herein, we report a straightforward, yet …

Ocular drug delivery: advancements and innovations

B Tian, E Bilsbury, S Doherty, S Teebagy, E Wood… - Pharmaceutics, 2022 - mdpi.com
Ocular drug delivery has been significantly advanced for not only pharmaceutical
compounds, such as steroids, nonsteroidal anti-inflammatory drugs, immune modulators …

Effective gene therapy of Stargardt disease with PEG-ECO/pGRK1-ABCA4-S/MAR nanoparticles

D Sun, W Sun, SQ Gao, J Lehrer, A Naderi… - … Therapy-Nucleic Acids, 2022 - cell.com
Stargardt disease (STGD) is the most common form of inherited retinal genetic disorders and
is often caused by mutations in ABCA4. Gene therapy has the promise to effectively treat …

[HTML][HTML] What's new in ocular drug delivery: advances in suprachoroidal injection since 2023

KY Wu, A Gao, M Giunta, SD Tran - Pharmaceuticals, 2024 - mdpi.com
Despite significant advancements in ocular drug delivery, challenges persist in treating
posterior segment diseases like macular edema (ME) and age-related macular …