[HTML][HTML] An update on Becker muscular dystrophy

V Straub, M Guglieri - Current Opinion in Neurology, 2023 - journals.lww.com
An update on Becker muscular dystrophy : Current Opinion in Neurology An update on Becker
muscular dystrophy : Current Opinion in Neurology Log in or Register Subscribe to …

Comparison of pharmaceutical properties and biological activities of prednisolone, deflazacort, and vamorolone in DMD disease models

G Liu, P Lipari, A Mollin, S Jung… - Human molecular …, 2024 - academic.oup.com
Duchenne muscular dystrophy (DMD) is a progressive disabling X-linked recessive disorder
that causes gradual and irreversible loss of muscle, resulting in early death. The …

The Potential of Targeting APE1/Ref-1 as a Therapeutic Intervention for Duchenne Muscular Dystrophy

H Lalunio, N Stupka, CA Goodman… - Antioxidants & Redox …, 2024 - liebertpub.com
Significance: Inflammation and oxidative stress play crucial roles in the development and
progression of skeletal muscle diseases. This review aims to examine the existing evidence …

Considering the promise of vamorolone for treating Duchenne muscular dystrophy

MD Grounds, EM Lloyd - Journal of Neuromuscular Diseases, 2023 - journals.sagepub.com
This commentary provides an independent consideration of data related to the drug
vamorolone (VBP15) as an alternative steroid proposed for treatment of Duchenne muscular …

[HTML][HTML] Becker muscular dystrophy

PK Thada, J Bhandari, KC Forshaw… - StatPearls …, 2024 - ncbi.nlm.nih.gov
Objectives: Apply the pathophysiology and symptomatology of Becker muscular dystrophy in
therapy selection. Determine the evaluation process for patients with suspected Becker …

The latest developments in synthetic approaches to duchenne muscular dystrophy

LM Johnson, TG Pulskamp… - Expert Review of …, 2025 - Taylor & Francis
Introduction Duchenne muscular dystrophy (DMD) is a rare X-linked genetic disorder
caused by mutations in the dystrophin gene, leading to an almost complete absence of …

Efficacy and safety of different doses of vamorolone in boys with Duchenne muscular dystrophy: a systematic review and network meta-analysis

Q Wang, Y Zeng, L Jiao, J He, B Li, Y Guo… - Frontiers in …, 2024 - frontiersin.org
Background and objectives Several recent clinical studies have indicated that vamorolone is
comparable in effectiveness to glucocorticosteroids for treating Duchenne muscular …

Efficacy and Safety of Vamorolone in Duchenne Muscular Dystrophy: A Systematic Review

C Pascual-Morena, M Lucerón-Lucas-Torres… - Pediatric Drugs, 2024 - Springer
Background Vamorolone has recently been approved for the management of Duchenne
muscular dystrophy to replace glucocorticosteroids, which theoretically have more side …

Getting Wheels–Development and Pilot Evaluation of a Booklet for Families When Introducing a Wheelchair to Children With a Neuromuscular Condition

SG Paguinto - 2024 - search.proquest.com
When walking is difficult to attain or maintain, the ability to mobilise independently with the
use of wheelchair equipment is often a positive and joyful experience for families of children …

Assessing the impact of Myomaker and Myomerger in mature muscle fibers

PC Witcher - 2023 - search.proquest.com
Skeletal muscle plays a pivotal role in everyday life. Not only does it allow locomotion but it
also helps with temperature regulation and a myriad of metabolic pathways. The organized …