Clinical trial design, end-points, and emerging therapies in pulmonary arterial hypertension

J Weatherald, TR Fleming, MR Wilkins… - European …, 2024 - publications.ersnet.org
Clinical trials in pulmonary arterial hypertension (PAH) have led to the approval of several
effective treatments that improve symptoms, exercise capacity and clinical outcomes. In …

The evolution of clinical trials for pediatric pulmonary hypertension: are the needs of patients and their caregivers being met?

J Wacker, R Joye, L Genecand, F Lador… - Expert Review of …, 2024 - Taylor & Francis
Introduction Pediatric pulmonary hypertension is a rare condition. Survival remains poor in
the current management era. There is a lack of data regarding the medical management of …

Analysis of Terminated Pulmonary Hypertension Clinical Trials. What Are We Doing Wrong?

M Abdulelah, ZA Abdulelah, M Azzam… - Current Problems in …, 2024 - Elsevier
Despite significant interest in the diagnosis and treatment of pulmonary hypertension (PH)
over the past two decades, there have been no notable advancements in reducing mortality …

Win Statistics in Pulmonary Arterial Hypertension Clinical Trials

J Weatherald, J Moutchia, N Al-Naamani… - American Journal of …, 2023 - atsjournals.org
Methods We performed a meta-analysis of individual participant data from 18 phase III
randomized clinical trials of therapies for PAH submitted to the US Food and Drug …

Ambitions for Pulmonary Arterial Hypertension Composite End Points: A Chain Is Only as Strong as Its Weakest Link

JGE Zelt, J Weatherald, SC Mathai - Chest, 2023 - journal.chestnet.org
The recent European Cardiology Society/European Respiratory Society clinical guidelines
for the treatment of pulmonary arterial hypertension (PAH) recommend that selection of …