Enhancers in disease: molecular basis and emerging treatment strategies

A Claringbould, JB Zaugg - Trends in molecular medicine, 2021 - cell.com
Enhancers are genomic sequences that play a key role in regulating tissue-specific gene
expression levels. An increasing number of diseases are linked to impaired enhancer …

Ensembl 2023

FJ Martin, MR Amode, A Aneja… - Nucleic acids …, 2023 - academic.oup.com
Abstract Ensembl (https://www. ensembl. org) has produced high-quality genomic resources
for vertebrates and model organisms for more than twenty years. During that time, our …

Genome interpretation using in silico predictors of variant impact

P Katsonis, K Wilhelm, A Williams, O Lichtarge - Human genetics, 2022 - Springer
Estimating the effects of variants found in disease driver genes opens the door to
personalized therapeutic opportunities. Clinical associations and laboratory experiments …

Emerging applications of machine learning in genomic medicine and healthcare

N Chafai, L Bonizzi, S Botti… - Critical Reviews in Clinical …, 2024 - Taylor & Francis
The integration of artificial intelligence technologies has propelled the progress of clinical
and genomic medicine in recent years. The significant increase in computing power has …

Computational approaches for predicting variant impact: An overview from resources, principles to applications

Y Liu, WSB Yeung, PCN Chiu, D Cao - Frontiers in genetics, 2022 - frontiersin.org
One objective of human genetics is to unveil the variants that contribute to human diseases.
With the rapid development and wide use of next-generation sequencing (NGS), massive …

VarCards2: an integrated genetic and clinical database for ACMG-AMP variant-interpretation guidelines in the human whole genome

Z Wang, G Zhao, Z Zhu, Y Wang, X **ang… - Nucleic Acids …, 2024 - academic.oup.com
VarCards, an online database, combines comprehensive variant-and gene-level annotation
data to streamline genetic counselling for coding variants. Recognising the increasing …

VPatho: a deep learning-based two-stage approach for accurate prediction of gain-of-function and loss-of-function variants

F Ge, C Li, S Iqbal, A Muhammad, F Li… - Briefings in …, 2023 - academic.oup.com
Determining the pathogenicity and functional impact (ie gain-of-function; GOF or loss-of-
function; LOF) of a variant is vital for unraveling the genetic level mechanisms of human …

SHINE: protein language model-based pathogenicity prediction for short inframe insertion and deletion variants

X Fan, H Pan, A Tian, WK Chung… - Briefings in …, 2023 - academic.oup.com
Accurate variant pathogenicity predictions are important in genetic studies of human
diseases. Inframe insertion and deletion variants (indels) alter protein sequence and length …

GoFCards: an integrated database and analytic platform for gain of function variants in humans

W Zhao, Y Tao, J **ong, L Liu, Z Wang… - Nucleic Acids …, 2025 - academic.oup.com
Abstract Gain-of-function (GOF) variants, which introduce new or amplify protein functions,
are essential for understanding disease mechanisms. Despite advances in genomics and …

Tissue-aware interpretation of genetic variants advances the etiology of rare diseases

CM Argov, A Shneyour, J Jubran, E Sabag… - Molecular Systems …, 2024 - embopress.org
Pathogenic variants underlying Mendelian diseases often disrupt the normal physiology of a
few tissues and organs. However, variant effect prediction tools that aim to identify …