Polyglutamine spinocerebellar ataxias—from genes to potential treatments

HL Paulson, VG Shakkottai, HB Clark… - Nature Reviews …, 2017 - nature.com
The dominantly inherited spinocerebellar ataxias (SCAs) are a large and diverse group of
neurodegenerative diseases. The most prevalent SCAs (SCA1, SCA2, SCA3, SCA6 and …

Autosomal dominant cerebellar ataxias: polyglutamine expansions and beyond

A Durr - The Lancet Neurology, 2010 - thelancet.com
Cerebellar ataxias with autosomal dominant transmission are rare, but identification of the
associated genes has provided insight into the mechanisms that could underlie other forms …

N omenclature of genetic movement disorders: R ecommendations of the international P arkinson and movement disorder society task force

C Marras, A Lang, BP van de Warrenburg… - Movement …, 2016 - Wiley Online Library
The system of assigning locus symbols to specify chromosomal regions that are associated
with a familial disorder has a number of problems when used as a reference list of …

The role of glutamate transporters in neurodegenerative diseases and potential opportunities for intervention

AL Sheldon, MB Robinson - Neurochemistry international, 2007 - Elsevier
Extracellular concentrations of the predominant excitatory neurotransmitter, glutamate, and
related excitatory amino acids are maintained at relatively low levels to ensure an …

Brain pathology of spinocerebellar ataxias

K Seidel, S Siswanto, ERP Brunt, W Den Dunnen… - Acta …, 2012 - Springer
The autosomal dominant cerebellar ataxias (ADCAs) represent a heterogeneous group of
neurodegenerative diseases with progressive ataxia and cerebellar degeneration. The …

Excitatory amino acid transporters in physiology and disorders of the central nervous system

AR Malik, TE Willnow - International journal of molecular sciences, 2019 - mdpi.com
Excitatory amino acid transporters (EAATs) encompass a class of five transporters with
distinct expression in neurons and glia of the central nervous system (CNS). EAATs are …

Transporters for L‐glutamate: An update on their molecular pharmacology and pathological involvement

PM Beart, RD O'Shea - British journal of pharmacology, 2007 - Wiley Online Library
l‐Glutamate (Glu) is the major excitatory neurotransmitter in the mammalian CNS and five
types of high‐affinity Glu transporters (EAAT1–5) have been identified. The transporters …

Developmental mechanism of the periodic membrane skeleton in axons

G Zhong, J He, R Zhou, D Lorenzo, HP Babcock… - Elife, 2014 - elifesciences.org
Actin, spectrin, and associated molecules form a periodic sub-membrane lattice structure in
axons. How this membrane skeleton is developed and why it preferentially forms in axons …

Pathogenic SPTBN1 variants cause an autosomal dominant neurodevelopmental syndrome

MA Cousin, BA Creighton, KA Breau, RC Spillmann… - Nature …, 2021 - nature.com
SPTBN1 encodes βII-spectrin, the ubiquitously expressed β-spectrin that forms micrometer-
scale networks associated with plasma membranes. Mice deficient in neuronal βII-spectrin …

Critical role of spectrin in hearing development and deafness

Y Liu, J Qi, X Chen, M Tang, C Chu, W Zhu, H Li… - Science …, 2019 - science.org
Inner ear hair cells (HCs) detect sound through the deflection of mechanosensory
stereocilia. Stereocilia are inserted into the cuticular plate of HCs by parallel actin rootlets …