Pre-twisting for improved genome modification and miRNA targeting

R Lu, G Chen - Trends in Biochemical Sciences, 2024 - cell.com
Two reports by Dhuri et al. and Oyaghire et al., respectively, show that, through installing
chiral centers at the backbone of the artificial nucleic acid, peptide nucleic acid (PNA) …

Peptide nucleic acids: Recent advancements and future opportunities in biomedical applications

A Sannigrahi, N De, D Bhunia, J Bhadra - Bioorganic Chemistry, 2025 - Elsevier
Peptide nucleic acids (PNA), synthetic molecules comprising a peptide-like backbone and
natural and unnatural nucleobases, have garnered significant attention for their potential …

Anti-gene oligonucleotide clamps invade dsDNA and downregulate huntingtin expression

T Umek, KE Lundin, MO Mowoe, Y Hao, S Roudi… - … Therapy Nucleic Acids, 2024 - cell.com
Anti-gene oligonucleotides belong to a group of therapeutic compounds, which, in contrast
to antisense oligonucleotides, bind to DNA. Clamp anti-gene oligonucleotides bind through …

Harnessing Peptide Nucleic Acids and the Eukaryotic Resolvase MOC1 for Programmable, Precise Generation of Double-Strand DNA Breaks

G Sivakrishna Rao, AH Saleh, F Melliti… - Analytical …, 2024 - ACS Publications
Programmable site-specific nucleases (SSNs) hold extraordinary promise to unlock myriad
gene editing applications in medicine and agriculture. However, develo** small and …

Impact of charges on the hybridization kinetics and thermal stability of PNA duplexes

M López-Tena, N Winssinger - Organic & Biomolecular Chemistry, 2024 - pubs.rsc.org
Peptide nucleic acid (PNA) is prominent artificial nucleic acid mimetic and modifications at
the-position of the peptidic backbone are known to further enhance the desirable …

Systemic in utero gene editing as a treatment for cystic fibrosis

AS Ricciardi, C Barone, R Putman, E Quijano, A Gupta… - bioRxiv, 2024 - biorxiv.org
In utero gene editing has the potential to modify disease causing genes in multiple
develo** tissues before birth, possibly allowing for normal organ development, disease …