CRISPR technology: A decade of genome editing is only the beginning

JY Wang, JA Doudna - Science, 2023‏ - science.org
The advent of clustered regularly interspaced short palindromic repeat (CRISPR) genome
editing, coupled with advances in computing and imaging capabilities, has initiated a new …

Importance of the pig as a human biomedical model

JK Lunney, A Van Goor, KE Walker… - Science translational …, 2021‏ - science.org
Pigs have substantial potential as biomedical models for studying human developmental
processes, congenital diseases, and pathogen response mechanisms in addition to utility as …

Design and testing of a humanized porcine donor for xenotransplantation

RP Anand, JV Layer, D Heja, T Hirose, G Lassiter… - Nature, 2023‏ - nature.com
Recent human decedent model studies, and compassionate xenograft use have explored
the promise of porcine organs for human transplantation. To proceed to human studies, a …

First clinical‐grade porcine kidney xenotransplant using a human decedent model

PM Porrett, BJ Orandi, V Kumar, J Houp… - American Journal of …, 2022‏ - Wiley Online Library
A radical solution is needed for the organ supply crisis, and the domestic pig is a promising
organ source. In preparation for a clinical trial of xenotransplantation, we developed an in …

CRISPR-Cas guides the future of genetic engineering

GJ Knott, JA Doudna - Science, 2018‏ - science.org
The diversity, modularity, and efficacy of CRISPR-Cas systems are driving a
biotechnological revolution. RNA-guided Cas enzymes have been adopted as tools to …

Progress in xenotransplantation: overcoming immune barriers

M Sykes, DH Sachs - Nature Reviews Nephrology, 2022‏ - nature.com
A major limitation of organ allotransplantation is the insufficient supply of donor organs.
Consequently, thousands of patients die every year while waiting for a transplant. Progress …

Ten things you should know about transposable elements

G Bourque, KH Burns, M Gehring, V Gorbunova… - Genome biology, 2018‏ - Springer
Transposable elements (TEs) are major components of eukaryotic genomes. However, the
extent of their impact on genome evolution, function, and disease remain a matter of intense …

Gene therapy clinical trials worldwide to 2017: An update

SL Ginn, AK Amaya, IE Alexander… - The journal of gene …, 2018‏ - Wiley Online Library
To date, almost 2600 gene therapy clinical trials have been completed, are ongoing or have
been approved worldwide. Our database brings together global information on gene therapy …

[HTML][HTML] CRISPR-Cas systems: Overview, innovations and applications in human disease research and gene therapy

Y Xu, Z Li - Computational and structural biotechnology journal, 2020‏ - Elsevier
Genome editing is the modification of genomic DNA at a specific target site in a wide variety
of cell types and organisms, including insertion, deletion and replacement of DNA, resulting …

Vascular tissue engineering: progress, challenges, and clinical promise

HHG Song, RT Rumma, CK Ozaki, ER Edelman… - Cell stem cell, 2018‏ - cell.com
Although the clinical demand for bioengineered blood vessels continues to rise, current
options for vascular conduits remain limited. The synergistic combination of emerging …