Down syndrome and the complexity of genome dosage imbalance

SE Antonarakis - Nature Reviews Genetics, 2017 - nature.com
Down syndrome (also known as trisomy 21) is the model human phenotype for all genomic
gain dosage imbalances, including microduplications. The functional genomic exploration of …

Transcriptome profiling in human diseases: new advances and perspectives

A Casamassimi, A Federico, M Rienzo… - International journal of …, 2017 - mdpi.com
In the last decades, transcriptome profiling has been one of the most utilized approaches to
investigate human diseases at the molecular level. Through expression studies, many …

Accelerated epigenetic aging in Down syndrome

S Horvath, P Garagnani, MG Bacalini, C Pirazzini… - Aging cell, 2015 - Wiley Online Library
Down Syndrome (DS) entails an increased risk of many chronic diseases that are typically
associated with older age. The clinical manifestations of accelerated aging suggest that …

Trisomy 21 consistently activates the interferon response

KD Sullivan, HC Lewis, AA Hill, A Pandey, LP Jackson… - Elife, 2016 - elifesciences.org
Although it is clear that trisomy 21 causes Down syndrome, the molecular events acting
downstream of the trisomy remain ill defined. Using complementary genomics analyses, we …

Domains of genome-wide gene expression dysregulation in Down's syndrome

A Letourneau, FA Santoni, X Bonilla, MR Sailani… - Nature, 2014 - nature.com
Trisomy 21 is the most frequent genetic cause of cognitive impairment. To assess the
perturbations of gene expression in trisomy 21, and to eliminate the noise of genomic …

RNA-Seq and human complex diseases: recent accomplishments and future perspectives

V Costa, M Aprile, R Esposito… - European Journal of …, 2013 - nature.com
The availability of the human genome sequence has allowed identification of disease-
causing mutations in many Mendelian disorders, and detection of significant associations of …

Mitochondrial dysfunction as a central actor in intellectual disability-related diseases: an overview of Down syndrome, autism, Fragile X and Rett syndrome

D Valenti, L de Bari, B De Filippis… - Neuroscience & …, 2014 - Elsevier
Clinical manifestations typical of mitochondrial diseases are often present in various genetic
syndromes associated with intellectual disability, a condition leading to deficit in cognitive …

Down syndrome: Neurobiological alterations and therapeutic targets

RA Vacca, S Bawari, D Valenti, D Tewari… - Neuroscience & …, 2019 - Elsevier
Down syndrome (DS) is a genetic disease that occurs due to an aneuploidy of human
chromosome 21. Trisomy of chromosome 21 is a primary genetic cause of developmental …

Next‐generation sequencing: ready for the clinics?

AN Desai, A Jere - Clinical genetics, 2012 - Wiley Online Library
Desai AN, Jere A. Next‐generation sequencing: ready for the clinics? Next‐generation
sequencing (NGS) has transformed genomic research by decreasing the cost of sequencing …

Trisomy of a Down syndrome critical region globally amplifies transcription via HMGN1 overexpression

CT Mowery, JM Reyes, L Cabal-Hierro, KJ Higby… - Cell reports, 2018 - cell.com
Summary Down syndrome (DS, trisomy 21) is associated with developmental abnormalities
and increased leukemia risk. To reconcile chromatin alterations with transcriptome changes …