Machine learning approaches to explore digenic inheritance

A Okazaki, J Ott - Trends in Genetics, 2022‏ - cell.com
Some rare genetic disorders, such as retinitis pigmentosa or Alport syndrome, are caused by
the co-inheritance of DNA variants at two different genetic loci (digenic inheritance). To …

[HTML][HTML] The Cardiofaciocutaneous syndrome: from genetics to prognostic–therapeutic implications

G Scorrano, E David, E Calì, R Chimenz, S La Bella… - Genes, 2023‏ - mdpi.com
Cardiofaciocutaneous (CFC) syndrome is one of the rarest RASopathies characterized by
multiple congenital ectodermal, cardiac and craniofacial abnormalities with a mild to severe …

GWAS meta-analysis of over 29,000 people with epilepsy identifies 26 risk loci and subtype-specific genetic architecture

Nature genetics, 2023‏ - nature.com
Epilepsy is a highly heritable disorder affecting over 50 million people worldwide, of which
about one-third are resistant to current treatments. Here we report a multi-ancestry genome …

High-impact rare genetic variants in severe schizophrenia

AW Zoghbi, RS Dhindsa, TE Goldberg… - Proceedings of the …, 2021‏ - pnas.org
Extreme phenotype sequencing has led to the identification of high-impact rare genetic
variants for many complex disorders but has not been applied to studies of severe …

Voltage‐gated calcium channels in genetic epilepsies

RJ Lauerer, H Lerche - Journal of Neurochemistry, 2024‏ - Wiley Online Library
Voltage‐gated calcium channels (VGCC) are abundant in the central nervous system and
serve a broad spectrum of functions, either directly in cellular excitability or indirectly to …

Genome-wide meta-analysis of over 29,000 people with epilepsy reveals 26 loci and subtype-specific genetic architecture

International League Against Epilepsy Consortium on … - MedRxiv, 2022‏ - medrxiv.org
Epilepsy is a highly heritable disorder affecting over 50 million people worldwide, of which
about one-third are resistant to current treatments. Here, we report a trans-ethnic GWAS …

Exome sequencing of 20,979 individuals with epilepsy reveals shared and distinct ultra-rare genetic risk across disorder subtypes

Nature neuroscience, 2024‏ - nature.com
Identifying genetic risk factors for highly heterogeneous disorders such as epilepsy remains
challenging. Here we present, to our knowledge, the largest whole-exome sequencing study …

[HTML][HTML] Technological and computational approaches to detect somatic mosaicism in epilepsy

CM Boßelmann, C Leu, D Lal - Neurobiology of Disease, 2023‏ - Elsevier
Lesional epilepsy is a common and severe disease commonly associated with
malformations of cortical development, including focal cortical dysplasia and …

Whole genome sequences discriminate hereditary hemorrhagic telangiectasia phenotypes by non-HHT deleterious DNA variation

KE Joyce, E Onabanjo, S Brownlow, F Nur… - Blood …, 2022‏ - ashpublications.org
The abnormal vascular structures of hereditary hemorrhagic telangiectasia (HHT) often
cause severe anemia due to recurrent hemorrhage, but HHT causal genes do not predict the …

Sporadic hypothalamic hamartoma is a ciliopathy with somatic and bi-allelic contributions

TE Green, JE Motelow, MF Bennett, Z Ye… - Human molecular …, 2022‏ - academic.oup.com
Hypothalamic hamartoma with gelastic seizures is a well-established cause of drug-resistant
epilepsy in early life. The development of novel surgical techniques has permitted the …