Trinucleotide repeat disorders

HT Orr, HY Zoghbi - Annu. Rev. Neurosci., 2007‏ - annualreviews.org
The discovery that expansion of unstable repeats can cause a variety of neurological
disorders has changed the landscape of disease-oriented research for several forms of …

Clinical features, neurogenetics and neuropathology of the polyglutamine spinocerebellar ataxias type 1, 2, 3, 6 and 7

U Rüb, L Schöls, H Paulson, G Auburger… - Progress in …, 2013‏ - Elsevier
The spinocerebellar ataxias type 1 (SCA1), 2 (SCA2), 3 (SCA3), 6 (SCA6) and 7 (SCA7) are
genetically defined autosomal dominantly inherited progressive cerebellar ataxias (ADCAs) …

Molecular pathogenesis of spinocerebellar ataxias

AM Duenas, R Goold, P Giunti - Brain, 2006‏ - academic.oup.com
The autosomal dominant spinocerebellar ataxias (SCAs) are a group of neurodegenerative
diseases, clinically and genetically heterogeneous, characterized by loss of balance and …

RORα-mediated Purkinje cell development determines disease severity in adult SCA1 mice

HG Serra, L Duvick, T Zu, K Carlson, S Stevens… - Cell, 2006‏ - cell.com
Summary Spinocerebellar ataxia type 1 (SCA1) is one of nine inherited, typically adult onset,
polyglutamine neurodegenerative diseases. To examine whether development impacts …

The Capicua repressor–a general sensor of RTK signaling in development and disease

G Jiménez, SY Shvartsman… - Journal of cell …, 2012‏ - journals.biologists.com
Receptor tyrosine kinase (RTK) signaling pathways control multiple cellular decisions in
metazoans, often by regulating the expression of downstream genes. In Drosophila …

The pathogenic mechanisms of polyglutamine diseases and current therapeutic strategies

PO Bauer, N Nukina - Journal of neurochemistry, 2009‏ - Wiley Online Library
Expansion of CAG trinucleotide repeat within the coding region of several genes results in
the production of proteins with expanded polyglutamine (PolyQ) stretch. The expression of …

Consensus paper: pathological mechanisms underlying neurodegeneration in spinocerebellar ataxias

A Matilla-Dueñas, T Ashizawa, A Brice, S Magri… - The Cerebellum, 2014‏ - Springer
Intensive scientific research devoted in the recent years to understand the molecular
mechanisms or neurodegeneration in spinocerebellar ataxias (SCAs) are identifying new …

Drosophila in the study of neurodegenerative disease

JL Marsh, LM Thompson - Neuron, 2006‏ - cell.com
As populations benefit from increasing lifespans, neurodegenerative diseases have
emerged as a critical health concern. How can the fruit fly, Drosophila melanogaster …

[HTML][HTML] CHIP protects from the neurotoxicity of expanded and wild-type ataxin-1 and promotes their ubiquitination and degradation

I Al-Ramahi, YC Lam, HK Chen, B de Gouyon… - Journal of Biological …, 2006‏ - Elsevier
CHIP (C terminus of Hsc-70 interacting protein) is an E3 ligase that links the protein folding
machinery with the ubiquitin-proteasome system and has been implicated in disorders …

The promise and perils of HDAC inhibitors in neurodegeneration

A Didonna, P Opal - Annals of clinical and translational …, 2015‏ - Wiley Online Library
Histone deacetylases (HDAC s) represent emerging therapeutic targets in the context of
neurodegeneration. Indeed, pharmacologic inhibition of HDAC s activity in the nervous …