REEV: review, evaluate and explain variants

D Hramyka, HL Sczakiel, MX Zhao… - Nucleic acids …, 2024‏ - academic.oup.com
In the era of high throughput sequencing, special software is required for the clinical
evaluation of genetic variants. We developed REEV (Review, Evaluate and Explain …

Computational facial analysis for rare Mendelian disorders

TC Hsieh, PM Krawitz - … Journal of Medical Genetics Part C …, 2023‏ - Wiley Online Library
With the advances in computer vision, computational facial analysis has become a powerful
and effective tool for diagnosing rare disorders. This technology, also called next‐generation …

[HTML][HTML] Clinical exome sequencing data from patients with inborn errors of immunity: Cohort level diagnostic yield and the benefit of systematic reanalysis

EE Vorsteveld, CI Van der Made, SP Smeekens… - Clinical …, 2024‏ - Elsevier
While next generation sequencing has expanded the scientific understanding of Inborn
Errors of Immunity (IEI), the clinical use and re-use of exome sequencing is still emerging …

GestaltGAN: Synthetic photorealistic portraits of individuals with rare genetic disorders

A Kirchhoff, A Hustinx, B Javanmardi… - European Journal of …, 2025‏ - nature.com
The facial gestalt (overall facial morphology) is a characteristic clinical feature in many
genetic disorders that is often essential for suspecting and establishing a specific diagnosis …

Understanding recessive disease risk in multi‐ethnic populations with different degrees of consanguinity

LA La Rocca, J Frank, HB Bentzen… - American Journal of …, 2024‏ - Wiley Online Library
Population medical genetics aims at translating clinically relevant findings from recent
studies of large cohorts into healthcare for individuals. Genetic counseling concerning …

Omics and rare diseases: challenges, applications, and future perspectives

D Braconi, H Nadwa, G Bernardini… - Expert Review of …, 2025‏ - Taylor & Francis
ABSTRACT Introduction Rare diseases (RDs) are a heterogeneous group of diseases
recognized as a relevant global health priority but posing aspects of complexity such as …

Next‐generation phenoty** in Nigerian children with Cornelia de Lange syndrome

A Arlt, A Knaus, TC Hsieh… - American Journal of …, 2024‏ - Wiley Online Library
Next‐generation phenoty** (NGP) can be used to compute the similarity of dysmorphic
patients to known syndromic diseases. So far, the technology has been evaluated in variant …

Privacy-by-Design with Federated Learning will drive future Rare Disease Research

S Süwer, MS Ullah, N Probul, A Maier… - Journal of …, 2024‏ - journals.sagepub.com
Up to 6% of the global population is estimated to be affected by one of about 10,000 distinct
rare diseases (RDs). RDs are, to this day, often not understood, and thus, patients are …

[HTML][HTML] Big data and transformative bioinformatics in genomic diagnostics and beyond

A Saparov, M Zech - Parkinsonism & Related Disorders, 2025‏ - Elsevier
The current era of high-throughput analysis-driven research offers invaluable insights into
disease etiologies, accurate diagnostics, pathogenesis, and personalized therapy. In the …

GestaltMatcher Database-A global reference for facial phenotypic variability in rare human diseases

H Lesmann, A Hustinx, S Moosa… - Research …, 2024‏ - pmc.ncbi.nlm.nih.gov
The most important factor that complicates the work of dysmorphologists is the significant
phenotypic variability of the human face. Next-Generation Phenoty** (NGP) tools that …