Advances of nanoparticles as drug delivery systems for disease diagnosis and treatment

R Liu, C Luo, Z Pang, J Zhang, S Ruan, M Wu… - Chinese chemical …, 2023 - Elsevier
Decades have passed since the first nanoparticles-base medicine was approved for human
cancer treatment, and the research and development of nanoparticles for drug delivery are …

The growth of siRNA-based therapeutics: Updated clinical studies

MM Zhang, R Bahal, TP Rasmussen… - Biochemical …, 2021 - Elsevier
More than two decades after the natural gene-silencing mechanism of RNA interference was
elucidated, small interfering RNA (siRNA)-based therapeutics have finally broken into the …

Therapeutic siRNA: state of the art

B Hu, L Zhong, Y Weng, L Peng, Y Huang… - Signal transduction and …, 2020 - nature.com
ABSTRACT RNA interference (RNAi) is an ancient biological mechanism used to defend
against external invasion. It theoretically can silence any disease-related genes in a …

[HTML][HTML] Pulmonary delivery of siRNA against acute lung injury/acute respiratory distress syndrome

M Zoulikha, Q **ao, GF Boafo, MA Sallam… - … Pharmaceutica Sinica B, 2022 - Elsevier
The use of small interfering RNAs (siRNAs) has been under investigation for the treatment of
several unmet medical needs, including acute lung injury/acute respiratory distress …

Membrane‐destabilizing ionizable lipid empowered imaging‐guided siRNA delivery and cancer treatment

S Guo, K Li, B Hu, C Li, M Zhang, A Hussain… - …, 2021 - Wiley Online Library
One of the imperative medical requirements for cancer treatment is how to establish an
imaging‐guided nanocarrier that combines therapeutic and imaging agents into one system …

In vivo gene delivery mediated by non-viral vectors for cancer therapy

R Mohammadinejad, A Dehshahri… - Journal of Controlled …, 2020 - Elsevier
Gene therapy by expression constructs or down-regulation of certain genes has shown great
potential for the treatment of various diseases. The wide clinical application of nucleic acid …

Small interfering RNA: Discovery, pharmacology and clinical development—An introductory review

P Ranasinghe, ML Addison, JW Dear… - British Journal of …, 2023 - Wiley Online Library
Post‐transcriptional gene silencing targets and degrades mRNA transcripts, silencing the
expression of specific genes. RNA interference technology, using synthetic structurally well …

A review of patisiran (ONPATTRO®) for the treatment of polyneuropathy in people with hereditary transthyretin amyloidosis

I Urits, D Swanson, MC Swett, A Patel, K Berardino… - Neurology and …, 2020 - Springer
Hereditary variant transthyretin amyloidosis (ATTRv) is a rare genetic defect that affects
about 5000–10,000 people worldwide, causing amyloidosis secondary to misfolding of …

The progress and promise of RNA medicine─ an arsenal of targeted treatments

JM Sasso, BJB Ambrose, R Tenchov… - Journal of medicinal …, 2022 - ACS Publications
In the past decade, there has been a shift in research, clinical development, and commercial
activity to exploit the many physiological roles of RNA for use in medicine. With the rapid …

The current status of gene therapy for the treatment of cancer

TM Belete - Biologics: Targets and Therapy, 2021 - Taylor & Francis
Gene therapy is the administration of foreign genomic material into the host tissue to modify
the expression of a gene product or to change the biological properties of cells for …