Defects in mRNA splicing and implications for infertility: a comprehensive review and in silico analysis

K Li, Y Chen, Y Sheng, D Tang, Y Cao… - Human Reproduction …, 2025‏ - academic.oup.com
BACKGROUND mRNA splicing is a fundamental process in the reproductive system,
playing a pivotal role in reproductive development and endocrine function, and ensuring the …

Estimating the sensitivity of genomic newborn screening for treatable inherited metabolic disorders

SL Bick, A Nathan, H Park, RC Green, MH Wojcik… - Genetics in …, 2025‏ - Elsevier
Purpose Over 30 research groups and companies are exploring newborn screening using
genomic sequencing (NBSeq), but the sensitivity of this approach is not well understood …

Linkage equilibrium between rare mutations

AS Lyulina, Z Liu, BH Good - Genetics, 2024‏ - academic.oup.com
Recombination breaks down genetic linkage by reshuffling existing variants onto new
genetic backgrounds. These dynamics are traditionally quantified by examining the …

Homozygous synonymous FAM111A variant underlies an autosomal recessive form of Kenny-Caffey syndrome

LD Bonde, IM Abdelrazek, L Seif, M Alawi… - Journal of Human …, 2024‏ - nature.com
FAM111A (family with sequence similarity 111 member A) is a serine protease and removes
covalent DNA-protein cross-links during DNA replication. Heterozygous gain-of-function …

Germline variants of homology‐directed repair or mismatch repair genes in cervical cancer

L Kokemüller, D Ramachandran… - … Journal of Cancer, 2025‏ - Wiley Online Library
While cervical cancer is associated with a persistent human papillomavirus (HPV) infection,
the progression to cancer is influenced by genomic risk factors that have remained largely …

The spectrum of gene intolerance to variation: Insights from a rare disease cohort

P Cacheiro, G Marengo, DU Gorkin, KA Peterson… - medRxiv, 2025‏ - medrxiv.org
Deciphering the spectrum of intolerance to loss-of-function (LoF) variation helps identify
genes that are critical at various stages of development and hierarchical levels of …

Missing genetic diversity impacts variant prioritisation for rare disorders

S Tallman, L Moutsianas, T Nguyen, Y Cho… - medRxiv, 2024‏ - medrxiv.org
Whole genome sequencing identifies millions of genetic variants per individual. When
applied to rare disease diagnosis, potentially pathogenic variants are prioritised for clinical …

The distribution of highly deleterious variants across human ancestry groups

A Stolyarova, G Coop, M Przeworski - bioRxiv, 2025‏ - biorxiv.org
A major focus of human genetics is to map severe disease mutations. Increasingly that goal
is understood as requiring huge numbers of people to be sequenced from every broadly …

IL-9 as a naturally orthogonal cytokine with optimal JAK/STAT signaling for engineered T cell therapy

H Jiang, S Limsuwannarot, KR Kulhanek, A Pal… - bioRxiv, 2025‏ - biorxiv.org
Arming T cells with a synthetically orthogonal IL-9 receptor (o9R) permits facile engraftment
and potent anti-tumor functions. We considered whether the paucity of natural IL-9R …

Pathogenetic mechanisms of muscle-specific ribosomes in dilated cardiomyopathy

MR Murphy, M Ganapathi, TM Lee, JM Fisher, MV Patel… - bioRxiv, 2025‏ - biorxiv.org
The heart employs a specialized ribosome in its muscle cells to translate genetic information
into proteins, a fundamental adaptation with an elusive physiological role. Its significance is …